Risdiplam in Presymptomatic Spinal Muscular Atrophy

Richard S. Finkel

Center for Experimental Neurotherapeutics, Department of Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, TN

Laurent Servais

MDUK (Muscular Dystrophy UK) Oxford Neuromuscular Centre and NIHR (National Institute for Health and Care Research) Oxford Biomedical Research Centre, University of Oxford, Oxford, United Kingdom

Dmitry Vlodavets

Russian Children Neuromuscular Center, Veltischev Clinical Pediatrics and Pediatric Surgery Research Institute of Pirogov Russian National Research Medical University, Moscow

Edmar Zanoteli

Department of Neurology, Faculdade de Medicina, Universidade de São Paulo, São Paulo

Maria Mazurkiewicz-Bełdzińska

Department of Developmental Neurology, Chair of Neurology, Medical University of Gdańsk, Gdańsk, Poland

Yuh-Jyh Jong

Aledie Navas-Nazario

Division of Pulmonology, Nemours Children’s Health Orlando, Orlando, FL

Mohammad Al-Muhaizea

Neuroscience Center, King Faisal Specialist Hospital and Research Center–Riyadh, Riyadh, Saudi Arabia

Alexandra P.Q.C. Araujo

Department of Pediatrics, Faculty of Medicine, Federal University of Rio de Janeiro, Rio de Janeiro

Leslie Nelson

Department of Physical Therapy, University of Texas Southwestern Medical Center, Dallas

Yi Wang

Birgit Jaber

Pharma Development Safety, F. Hoffmann–La Roche, Basel, Switzerland

Ksenija Gorni

Product Development Medical Affairs, Neuroscience and Rare Disease, F. Hoffmann–La Roche, Basel, Switzerland

Heidemarie Kletzl

Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, Basel, Switzerland

Laura Palfreeman

Roche Products, Welwyn Garden City, United Kingdom

Michael Rabbia

Genentech, South San Francisco, CA

Dave Summers

Roche Products, Welwyn Garden City, United Kingdom

Eleni Gaki

Roche Products, Welwyn Garden City, United Kingdom

Kathryn R. Wagner

Pharma Development Neurology, F. Hoffmann–La Roche, Basel, Switzerland

Paulo Fontoura

Product Development Medical Affairs, Neuroscience and Rare Disease, F. Hoffmann–La Roche, Basel, Switzerland

Michelle A. Farrar

Department of Neurology, Sydney Children’s Hospital Network, Sydney

Enrico Bertini

Research Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children’s Research Hospital IRCCS, Rome