Risdiplam in Presymptomatic Spinal Muscular Atrophy - Richard S. Finkel; Laurent Servais; Dmitry Vlodavets; Edmar Zanoteli; Maria Mazurkiewicz-Bełdzińska; Yuh-Jyh Jong; Aledie Navas-Nazario; Mohammad Al-Muhaizea; Alexandra P.Q.C. Araujo; Leslie Nelson; Yi Wang; Birgit Jaber; et al. (New England Journal of Medicine, 2025)