Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency

Claire Booth

University College London Great Ormond Street Institute of Child Health, London

Katelyn Masiuk

Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles

Konstantinos Vazouras

University College London Great Ormond Street Institute of Child Health, London

Augustine Fernandes

Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles

Jinhua Xu-Bayford

Department of Paediatric Immunology and Gene Therapy, Great Ormond Street Hospital for Sick Children NHS Foundation Trust, London

Beatriz Campo Fernandez

Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles

Sohini Roy

Beatrice Curio-Penny

Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles

Jordyn Arnold

Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles

Dayna Terrazas

Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles

Jack Reid

Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles

Kimberly C. Gilmour

Department of Immunology, National Institute for Health and Care Research Great Ormond Street Hospital Biomedical Research Centre, London

Stuart Adams

Great Ormond Street Hospital for Children NHS Trust, London

Elena Alvarez Mediavilla

University College London Great Ormond Street Institute of Child Health, London

Lana Mhaldien

Department of Immunology, National Institute for Health and Care Research Great Ormond Street Hospital Biomedical Research Centre, London

Grainne O’Toole

Department of Paediatric Immunology and Gene Therapy, Great Ormond Street Hospital for Sick Children NHS Foundation Trust, London

Rima Ahmed

Department of Paediatric Immunology and Gene Therapy, Great Ormond Street Hospital for Sick Children NHS Foundation Trust, London

Elizabeth Garabedian

National Human Genome Research Institute, National Institutes of Health, Bethesda, MD

Harry Malech

Section of Genetic Immunotherapy, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD

Suk See De Ravin

Theodore B. Moore

Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles

Satiro De Oliveira

Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles

Danilo Pellin

Tsai-Yu Lin

Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis

Thao Thi Dang

Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis

Kenneth Cornetta

Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis

Michael S. Hershfield

Duke University Medical Center, Durham, North Carolina

Havinder Hara

University College London Great Ormond Street Institute of Child Health, London

Adrian J. Thrasher

University College London Great Ormond Street Institute of Child Health, London

H. Bobby Gaspar

University College London Great Ormond Street Institute of Child Health, London

Donald B. Kohn

Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles