Booth, C., Masiuk, K., Vazouras, K., Fernandes, A., Xu-Bayford, J., Fernandez, B. C., Roy, S., Curio-Penny, B., Arnold, J., Terrazas, D., Reid, J., Gilmour, K. C., Adams, S., Mediavilla, E. A., Mhaldien, L., O’Toole, G., Ahmed, R., Garabedian, E., Malech, H., Ravin, S. S. D., Moore, T. B., Oliveira, S. D., Pellin, D., Lin, T., Dang, T. T., Cornetta, K., Hershfield, M. S., Hara, H., Thrasher, A. J., Gaspar, H. B., Kohn, D. B. (2025). Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency. New England Journal of Medicine. https://doi.org/10.1056/nejmoa2502754