Genetic suppression features ABHD18 as a Barth syndrome therapeutic target

S Sanna N. Masud A Anchal Srivastava P Patricia Mero V Victoria Saba Echezarreta E Eve Anderson L Lennard van Buren J Jiarun Wei D David Thomson Taylor A Adrian Granda Farias N Nicholas Mikolajewicz A Angela Shaw B Brandon M. Murareanu M Michelle Lohbihler O Olivia Sniezek Carney S Simon van Heeringen L Linda Clijsters O Olga Sizova J Jeroen van Ameijde F Freya Nye A Andrea Habsid L Lucy Nedyalkova L Laura McDonald C Craig Simpson L Leanne Wybenga-Groot K Kevin R. Brown N Nhi Nho R Radu M. Suciu K Katherine Chan A Amy H. Y. Tong F Frédéric M. Vaz B Bastiaan Evers R Robert Lesurf T Tanya Papaz L Lauryl M. J. Nutter S Stephanie Protze M Maximilian Billmann M Michael Costanzo B Brenda J. Andrews C Chad L. Myers S Seema Mital H Hilary Vernon T Thijn R. Brummelkamp C Charles Boone I Ian C. Scott M Micah J. Niphakis D Douglas Strathdee S Sebastian M. B. Nijman V Vincent A. Blomen J Jason Moffat

Article Details

Journal Nature
Volume / Issue Vol. 645, Issue 8082
Published September 25, 2025
Pages 1029-1038
ISSN 0028-0836
Publisher Nature Portfolio

Journal Info

Nature

Nature Portfolio

ISSN: 0028-0836 Health Sciences

Authors (49)

S

Sanna N. Masud

A

Anchal Srivastava

P

Patricia Mero

V

Victoria Saba Echezarreta

E

Eve Anderson

L

Lennard van Buren

J

Jiarun Wei

D

David Thomson Taylor

A

Adrian Granda Farias

N

Nicholas Mikolajewicz

A

Angela Shaw

B

Brandon M. Murareanu

M

Michelle Lohbihler

O

Olivia Sniezek Carney

S

Simon van Heeringen

L

Linda Clijsters

O

Olga Sizova

J

Jeroen van Ameijde

F

Freya Nye

A

Andrea Habsid

L

Lucy Nedyalkova

L

Laura McDonald

C

Craig Simpson

L

Leanne Wybenga-Groot

K

Kevin R. Brown

N

Nhi Nho

R

Radu M. Suciu

K

Katherine Chan

A

Amy H. Y. Tong

F

Frédéric M. Vaz

B

Bastiaan Evers

R

Robert Lesurf

T

Tanya Papaz

L

Lauryl M. J. Nutter

S

Stephanie Protze

M

Maximilian Billmann

M

Michael Costanzo

B

Brenda J. Andrews

C

Chad L. Myers

S

Seema Mital

H

Hilary Vernon

T

Thijn R. Brummelkamp

C

Charles Boone

I

Ian C. Scott

M

Micah J. Niphakis

D

Douglas Strathdee

S

Sebastian M. B. Nijman

V

Vincent A. Blomen

J

Jason Moffat