Engasertib versus Placebo for Bleeding in Hereditary Hemorrhagic Telangiectasia

H Hanny Al-Samkari (Department of Medicine, Massachusetts General Hospital, Boston) J Josefien Hessels (Department of Pulmonology, St. Antonius Hospital, Nieuwegein, the Netherlands) A Antoni Riera-Mestre (Department of Internal Medicine, Hospital Universitari de Bellvitge–Institut d’Investigació Biomèdica de Bellvitge, L’Hospitalet de Llobregat, Spain) S Sophie Dupuis-Girod (Genetic Department, Hôpital Femme–Mère–Enfant, Hospices Civils de Lyon, Bron, France) T Thibaut Van Zele (Department of Otorhinolaryngology, Ghent University Hospital, Ghent, Belgium) V Vicente Gómez del Olmo (Internal Medicine Department, Ramón y Cajal University Hospital, Instituto Ramón y Cajal de Investigación Sanitaria, Madrid) P Pamela G. Hodges (Division of Hematology–Oncology, Massachusetts General Hospital, Harvard Medical School, Boston) R Raquel Torres-Iglesias (Department of Internal Medicine, Hospital Universitari de Bellvitge–Institut d’Investigació Biomèdica de Bellvitge, L’Hospitalet de Llobregat, Spain) R Roberto Bertè (Gastroenterology Department, Azienda Socio-Sanitaria Territoriale, Ospedale Maggiore Crema, Crema, Italy) P Pierre Saint-Mezard (Vaderis Therapeutics, Basel, Switzerland) H Hedvika Lazar (Vaderis Therapeutics, Basel, Switzerland) N Nicholas Benedict (Vaderis Therapeutics, Basel, Switzerland) D Debra Barker (Vaderis Therapeutics, Basel, Switzerland) C Corrado Bernasconi (Vaderis Therapeutics, Basel, Switzerland) D Damien Picard (Vaderis Therapeutics, Basel, Switzerland) E Elisabetta Buscarini (Gastroenterology Department, Azienda Socio-Sanitaria Territoriale, Ospedale Maggiore Crema, Crema, Italy) H Hans-Jurgen Mager (Department of Pulmonology, St. Antonius Hospital, Nieuwegein, the Netherlands)

Article Details

Volume / Issue Vol. 393, Issue 21
Published November 27, 2025
Pages 2131-2141
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (17)

H

Hanny Al-Samkari

Department of Medicine, Massachusetts General Hospital, Boston

J

Josefien Hessels

Department of Pulmonology, St. Antonius Hospital, Nieuwegein, the Netherlands

A

Antoni Riera-Mestre

Department of Internal Medicine, Hospital Universitari de Bellvitge–Institut d’Investigació Biomèdica de Bellvitge, L’Hospitalet de Llobregat, Spain

S

Sophie Dupuis-Girod

Genetic Department, Hôpital Femme–Mère–Enfant, Hospices Civils de Lyon, Bron, France

T

Thibaut Van Zele

Department of Otorhinolaryngology, Ghent University Hospital, Ghent, Belgium

V

Vicente Gómez del Olmo

Internal Medicine Department, Ramón y Cajal University Hospital, Instituto Ramón y Cajal de Investigación Sanitaria, Madrid

P

Pamela G. Hodges

Division of Hematology–Oncology, Massachusetts General Hospital, Harvard Medical School, Boston

R

Raquel Torres-Iglesias

Department of Internal Medicine, Hospital Universitari de Bellvitge–Institut d’Investigació Biomèdica de Bellvitge, L’Hospitalet de Llobregat, Spain

R

Roberto Bertè

Gastroenterology Department, Azienda Socio-Sanitaria Territoriale, Ospedale Maggiore Crema, Crema, Italy

P

Pierre Saint-Mezard

Vaderis Therapeutics, Basel, Switzerland

H

Hedvika Lazar

Vaderis Therapeutics, Basel, Switzerland

N

Nicholas Benedict

Vaderis Therapeutics, Basel, Switzerland

D

Debra Barker

Vaderis Therapeutics, Basel, Switzerland

C

Corrado Bernasconi

Vaderis Therapeutics, Basel, Switzerland

D

Damien Picard

Vaderis Therapeutics, Basel, Switzerland

E

Elisabetta Buscarini

Gastroenterology Department, Azienda Socio-Sanitaria Territoriale, Ospedale Maggiore Crema, Crema, Italy

H

Hans-Jurgen Mager

Department of Pulmonology, St. Antonius Hospital, Nieuwegein, the Netherlands