Al-Samkari, H., Hessels, J., Riera-Mestre, A., Dupuis-Girod, S., Zele, T. V., Olmo, V. G. D., Hodges, P. G., Torres-Iglesias, R., Bertè, R., Saint-Mezard, P., Lazar, H., Benedict, N., Barker, D., Bernasconi, C., Picard, D., Buscarini, E., Mager, H. (2025). Engasertib versus Placebo for Bleeding in Hereditary Hemorrhagic Telangiectasia. New England Journal of Medicine. https://doi.org/10.1056/nejmoa2504411