An Intravenous Brain-Penetrant Enzyme Therapy for Mucopolysaccharidosis II
Article Details
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
Authors (16)
Joseph Muenzer
University of North Carolina School of Medicine, Chapel Hill
Barbara K. Burton
Ann and Robert H. Lurie Children’s Hospital of Chicago, Northwestern University, Chicago
Paul Harmatz
UCSF Benioff Children’s Hospital Oakland, Oakland, CA
Deepa S. Rajan
UPMC Children’s Hospital of Pittsburgh, University of Pittsburgh, Pittsburgh
Simon A. Jones
Systems Immunity Research Institute and Division of Infection and Immunity, School of Medicine, Cardiff University
Johanna M.P. van den Hout
Erasmus University Medical Center, Rotterdam, the Netherlands
John J. Mitchell
Montreal Children’s Hospital, McGill University Health Centre, Montreal
Akhil Bhalla
Denali Therapeutics, South San Francisco, CA
Natalie J. Engmann
Denali Therapeutics, South San Francisco, CA
Imanol Zubizarreta
Denali Therapeutics, South San Francisco, CA
Wei Dong
Hangzhou Institute of Medicine Chinese Academy of Sciences
Fabian Model
Denali Therapeutics, South San Francisco, CA
Ryan J. Watts
Denali Therapeutics, South San Francisco, CA
Matthew D. Troyer
Denali Therapeutics, South San Francisco, CA
Peter S. Chin
Denali Therapeutics, South San Francisco, CA
Carole Ho