Muenzer, J., Burton, B. K., Harmatz, P., Rajan, D. S., Jones, S. A., Hout, J. M. V. D., Mitchell, J. J., Bhalla, A., Engmann, N. J., Zubizarreta, I., Dong, W., Model, F., Watts, R. J., Troyer, M. D., Chin, P. S., Ho, C. (2026). An Intravenous Brain-Penetrant Enzyme Therapy for Mucopolysaccharidosis II. New England Journal of Medicine. https://doi.org/10.1056/nejmoa2508681