AAV9-Mediated Gene Therapy for Infantile-Onset Pompe’s Disease
Article Details
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
Authors (28)
Xiuwei Ma
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing
Lu Zhuang
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing
Wenhao Ma
Genecradle Therapeutics, Beijing
Jun Li
Yingying Mao
Genecradle Therapeutics, Beijing
Jianhua Wang
Xiaodong Wang
CAS Key Laboratory of Science and Technology on Applied Catalysis
Juan Xu
Shanghai Engineering Research Center of Biotransformation of Organic Solid Waste, School of Ecological and Environmental Sciences
Shuangqing Yu
Genecradle Therapeutics, Beijing
Ruijie Gu
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing
Yongxia Wang
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing
Zhongqiu Li
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing
Xinyang Jiang
Zhongshan Institute for Drug Discovery
Sheng Zhang
Fang He
Xiao Yang
Lina Zhu
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing
Shan Zhang
Yanping Zhang
Ting Li
Qiuping Li
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing
Zhijie Wu
Genecradle Therapeutics, Beijing
Cengceng Zhang
Genecradle Therapeutics, Beijing
Yiying Zhang
Xiaoyan Dong
Genecradle Therapeutics, Beijing
Hui Xiong
Xiaobing Wu
Zhichun Feng
Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing