AAV9-Mediated Gene Therapy for Infantile-Onset Pompe’s Disease

X Xiuwei Ma (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing) L Lu Zhuang (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing) W Wenhao Ma (Genecradle Therapeutics, Beijing) J Jun Li Y Yingying Mao (Genecradle Therapeutics, Beijing) J Jianhua Wang X Xiaodong Wang (CAS Key Laboratory of Science and Technology on Applied Catalysis) J Juan Xu (Shanghai Engineering Research Center of Biotransformation of Organic Solid Waste, School of Ecological and Environmental Sciences) S Shuangqing Yu (Genecradle Therapeutics, Beijing) R Ruijie Gu (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing) Y Yongxia Wang (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing) Z Zhongqiu Li (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing) X Xinyang Jiang (Zhongshan Institute for Drug Discovery) S Sheng Zhang F Fang He X Xiao Yang L Lina Zhu (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing) S Shan Zhang Y Yanping Zhang T Ting Li Q Qiuping Li (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing) Z Zhijie Wu (Genecradle Therapeutics, Beijing) C Cengceng Zhang (Genecradle Therapeutics, Beijing) Y Yiying Zhang X Xiaoyan Dong (Genecradle Therapeutics, Beijing) H Hui Xiong X Xiaobing Wu Z Zhichun Feng (Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing)

Article Details

Volume / Issue Vol. 392, Issue 24
Published June 26, 2025
Pages 2438-2446
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (28)

X

Xiuwei Ma

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing

L

Lu Zhuang

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing

W

Wenhao Ma

Genecradle Therapeutics, Beijing

J

Jun Li

Y

Yingying Mao

Genecradle Therapeutics, Beijing

J

Jianhua Wang

X

Xiaodong Wang

CAS Key Laboratory of Science and Technology on Applied Catalysis

J

Juan Xu

Shanghai Engineering Research Center of Biotransformation of Organic Solid Waste, School of Ecological and Environmental Sciences

S

Shuangqing Yu

Genecradle Therapeutics, Beijing

R

Ruijie Gu

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing

Y

Yongxia Wang

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing

Z

Zhongqiu Li

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing

X

Xinyang Jiang

Zhongshan Institute for Drug Discovery

S

Sheng Zhang

F

Fang He

X

Xiao Yang

L

Lina Zhu

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing

S

Shan Zhang

Y

Yanping Zhang

T

Ting Li

Q

Qiuping Li

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing

Z

Zhijie Wu

Genecradle Therapeutics, Beijing

C

Cengceng Zhang

Genecradle Therapeutics, Beijing

Y

Yiying Zhang

X

Xiaoyan Dong

Genecradle Therapeutics, Beijing

H

Hui Xiong

X

Xiaobing Wu

Z

Zhichun Feng

Department of Pediatrics, Chinese People’s Liberation Army (PLA) General Hospital, Beijing