AAV9-Mediated Gene Therapy for Infantile-Onset Pompe’s Disease - Xiuwei Ma; Lu Zhuang; Wenhao Ma; Jun Li; Yingying Mao; Jianhua Wang; Xiaodong Wang; Juan Xu; Shuangqing Yu; Ruijie Gu; Yongxia Wang; Zhongqiu Li; et al. (New England Journal of Medicine, 2025)