Tamsulosin ameliorates bone loss by inhibiting the release of Cl <sup>−</sup> through wedging into an allosteric site of TMEM16A

S Shiliang Li (Beijing National Laboratory for Condensed Matter Physics) W Weijia Sun (National Key Laboratory of Space Medicine, China Astronaut Research and Training Center) S Shuang Li L Lili Zhu (Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology) S Shuai Guo (Department of Chemistry) J Jiaqi He (Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology) Y Yuheng Li (State Key Laboratory of Structural Chemistry) C Chaoquan Tian (Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology) Z Zhenjiang Zhao (Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology) T Tao Yu J Jianwei Li (Macao Institute of Materials Science and Engineering (MIMSE), Faculty of Innovation Engineering, Macau University of Science and Technology, Taipa, 999078 Macao, China) Y Yiqing Zhang (Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology) Y Youlong Hai (Department of Urology, Shanghai Sixth People’s Hospital Affiliated to Shanghai Jiao Tong University School of Medicine) J Jiawen Wang (Institute of Functional Nano & Soft Materials (FUNSOM)) Y Yongjun Zheng (Jiangsu Engineering Laboratory of Smart Carbon-Rich Materials and Device, Jiangsu Province Hi-Tech Key Laboratory for Bio-Medical Research, School of Chemistry and Chemical Engineering, Medical School) R Rui Wang X Xiaoyong Hu (Department of Urology, Shanghai Sixth People’s Hospital Affiliated to Shanghai Jiao Tong University School of Medicine) S Shukuan Ling (Oujiang Laboratory (Zhejiang Lab for Regenerative Medicine Vision and Brain Health)) H Honglin Li (Innovation Center for AI and Drug Discovery, School of Pharmacy, East China Normal University) Y Yingxian Li (National Key Laboratory of Space Medicine, China Astronaut Research and Training Center)

Abstract

TMEM16A, a key calcium-activated chloride channel, is crucial for many physiological and pathological processes such as cancer, hypertension, and osteoporosis, etc. However, the regulatory mechanism of TMEM16A is poorly understood, limiting the discovery of effective modulators. Here, we unveil an allosteric gating mechanism by presenting a high-resolution cryo-EM structure of TMEM16A in complex with a channel inhibitor that we identified, Tamsulosin, which is resolved at 2.93 Å. Tamsulosin wedges itself into a pocket within the extracellular domain of TMEM16A, surrounded by α1-α2, α5-α6, and α9-α10 loops. This binding stabilizes a transient preopen conformation of TMEM16A, which is activated by Ca 2+ ions while still preserving a closed pore to prevent Cl − permeation. Validation of this binding site through computational, electrophysiological, and functional experiments, along with site-directed mutagenesis, confirmed the pivotal roles of the pocket-lining residues R605 and E624 on α5-α6 loop in modulating Tamsulosin binding and pore activity. Tamsulosin induces significant positional shifts in extracellular loops, particularly the α5-α6 loop, which moves toward the extracellular exit of the pore, leading to noticeable structural rearrangements in pore-lining helices. The hinges induced by P595 in α5 and G711 in α7 introduce flexibility to the transmembrane helices, orienting Y593 to collaborate with I641 in effectively gating the preopening pore. Notably, Tamsulosin demonstrates significant antiosteoporotic effects by inhibiting TMEM16A, suggesting potential for its repurposing in new therapeutic indications. Our study not only enhances our understanding of the gating mechanism of TMEM16A inhibition but also facilitates structure-based drug design targeting TMEM16A.

Article Details

Volume / Issue Vol. 122, Issue 1
Published January 07, 2025
ISSN 0027-8424
Publisher National Academy of Sciences

Authors (20)

S

Shiliang Li

Beijing National Laboratory for Condensed Matter Physics

W

Weijia Sun

National Key Laboratory of Space Medicine, China Astronaut Research and Training Center

S

Shuang Li

L

Lili Zhu

Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology

S

Shuai Guo

Department of Chemistry

J

Jiaqi He

Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology

Y

Yuheng Li

State Key Laboratory of Structural Chemistry

C

Chaoquan Tian

Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology

Z

Zhenjiang Zhao

Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology

T

Tao Yu

J

Jianwei Li

Macao Institute of Materials Science and Engineering (MIMSE), Faculty of Innovation Engineering, Macau University of Science and Technology, Taipa, 999078 Macao, China

Y

Yiqing Zhang

Shanghai Key Laboratory of New Drug Design, School of Pharmacy, East China University of Science and Technology

Y

Youlong Hai

Department of Urology, Shanghai Sixth People’s Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

J

Jiawen Wang

Institute of Functional Nano & Soft Materials (FUNSOM)

Y

Yongjun Zheng

Jiangsu Engineering Laboratory of Smart Carbon-Rich Materials and Device, Jiangsu Province Hi-Tech Key Laboratory for Bio-Medical Research, School of Chemistry and Chemical Engineering, Medical School

R

Rui Wang

X

Xiaoyong Hu

Department of Urology, Shanghai Sixth People’s Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

S

Shukuan Ling

Oujiang Laboratory (Zhejiang Lab for Regenerative Medicine Vision and Brain Health)

H

Honglin Li

Innovation Center for AI and Drug Discovery, School of Pharmacy, East China Normal University

Y

Yingxian Li

National Key Laboratory of Space Medicine, China Astronaut Research and Training Center