Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B

Ulrike M. Reiss

Department of Hematology, St. Jude Children’s Research Hospital, Memphis, TN

Andrew M. Davidoff

Department of Surgery, St. Jude Children’s Research Hospital, Memphis, TN

Edward G.D. Tuddenham

Katharine Dormandy Haemophilia and Thrombosis Unit, Royal Free Hospital, London

Pratima Chowdary

Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, Department of Haematology, Cancer Institute, University College London, London

Jenny McIntosh

Cancer Institute, University College London, London

Vincent Muczynski

Cancer Institute, University College London, London

Malo Journou

Cancer Institute, University College London, London

Giulia Simini

Cancer Institute, University College London, London

Lydia Ireland

Cancer Institute, University College London, London

Saira Mohamed

Cancer Institute, University College London, London

Anne Riddell

Katharine Dormandy Haemophilia and Thrombosis Unit, Royal Free Hospital, London

Arnulfo J. Pie

Katharine Dormandy Haemophilia and Thrombosis Unit, Royal Free Hospital, London

Andrew Hall

Sheila Sherlock Liver Centre, Royal Free Hospital, London

Alberto Quaglia

Sheila Sherlock Liver Centre, Royal Free Hospital, London

Sarah Mangles

Basingstoke and North Hampshire Hospital NHS Foundation Trust, Basingstoke, United Kingdom

Johnny Mahlangu

Department of Molecular Medicine and Haematology, Faculty of Health Sciences, University of the Witwatersrand and National Health Laboratory Service, Johannesburg

Kristina Haley

Hemostasis and Thrombosis Center, Oregon Health and Science University, Portland

Michael Recht

Yale School of Medicine, New Haven, CT

Yu-Min Shen

Department of Internal Medicine, University of Texas Southwestern Medical Center, Dallas

Kathleen G. Halka

Baylor Scott and White Healthcare, Temple Clinic, Temple, TX

Gail Fortner

Department of Hematology, St. Jude Children’s Research Hospital, Memphis, TN

Christopher L. Morton

Department of Surgery, St. Jude Children’s Research Hospital, Memphis, TN

Zhengming Gu

Department of Pathology, St. Jude Children’s Research Hospital, Memphis, TN

Randall T. Hayden

Department of Pathology, St. Jude Children’s Research Hospital, Memphis, TN

Ellis J. Neufeld

Department of Hematology, St. Jude Children’s Research Hospital, Memphis, TN

Victoria I. Okhomina

Department of Biostatistics, St. Jude Children’s Research Hospital, Memphis, TN

Guolian Kang

Department of Biostatistics, St. Jude Children’s Research Hospital, Memphis, TN

Amit C. Nathwani

Katharine Dormandy Haemophilia and Thrombosis Unit, Royal Free Hospital, London