Specificity of CRISPR-Cas9 Editing in Exagamglogene Autotemcel — Update

A Angela Yen (Vertex Pharmaceuticals, Boston) T Tony Boitano (Vertex Pharmaceuticals, Boston) Z Zachary Zappala (Vertex Pharmaceuticals, Boston) S Sudipta Mahajan (Vertex Pharmaceuticals, Boston) T Thomas Willems (Vertex Pharmaceuticals, Boston) T Timothy D. Majarian (Vertex Pharmaceuticals, Boston) P Preethi Thunga (Vertex Pharmaceuticals, Boston) D David Altshuler (Vertex Pharmaceuticals, Boston)

Article Details

Volume / Issue Vol. 393, Issue 14
Published October 09, 2025
Pages 1440-1442
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (8)

A

Angela Yen

Vertex Pharmaceuticals, Boston

T

Tony Boitano

Vertex Pharmaceuticals, Boston

Z

Zachary Zappala

Vertex Pharmaceuticals, Boston

S

Sudipta Mahajan

Vertex Pharmaceuticals, Boston

T

Thomas Willems

Vertex Pharmaceuticals, Boston

T

Timothy D. Majarian

Vertex Pharmaceuticals, Boston

P

Preethi Thunga

Vertex Pharmaceuticals, Boston

D

David Altshuler

Vertex Pharmaceuticals, Boston