Safety and efficacy of elranatamab in patients with relapsed and/or refractory immunoglobulin light-chain amyloidosis

P Pedro Vianna (1Dana-Farber Cancer Institute, Jerome Lipper Multiple Myeloma Center, Department of Medical Oncology, Boston, United States) R Rajshekhar Chakraborty (1Department of Medicine, Columbia University Irving Medical Center, New York, NY) S Shahrier Hossain (1Dana-Farber Cancer Institute, Jerome Lipper Multiple Myeloma Center, Department of Medical Oncology, Boston, United States) D Divaya Bhutani (Columbia University Medical Center, New York) S Shannon Miller A Annemarie Rossi (2Department of Medical Oncology, Jerome Lipper Multiple Myeloma Center, Dana-Farber Cancer Institute, Boston, MA) S Sarah A. M. Cuddy (3Harvard Medical School, Boston, MA) R Rodney H. Falk (From the Department of Medicine, Northwestern Memorial Hospital, Chicago (C.W.Y.); and the Departments of Medicine (J.S.G., A.J.Y.), Radiology (B.G.G.), and Pathology (B.M.H.), Massachusetts General Hospital, the Departments of Medicine (J.S.G., R.H.F., A.J.Y.), Radiology (B.G.G.), and Pathology (B.M.H.), Harvard Medical School, and the Department of Medicine, Brigham and Women’s Hospital (R.H.F.) — all in Boston.) S Suzanne Lentzsch (Columbia University Medical Center, New York, New York, United States) J Jacob P. Laubach G Giada Bianchi

Abstract

Abstract Immunoglobulin light-chain (AL) amyloidosis is a plasma cell disorder characterized by progressive organ dysfunction secondary to deposition of organized immunoglobulin light-chain aggregates. Achievement of rapid and deep normalization of involved immunoglobulin free light chains is necessary to maximize chances of reversibility of organ dysfunction, which, in turn, results in improved quality and length of life. There are no US Food and Drug Administration (FDA)–approved therapies for patients with relapsed AL amyloidosis. B-cell maturation antigen–targeting (BCMA)-bispecific T-cell engagers teclistamab and elranatamab have shown high activity and acceptable safety profile in patients with relapsed and/or refractory multiple myeloma, leading to their FDA approval. Herein, we report on safety and efficacy of elranatamab for patients with relapsed and/or refractory AL amyloidosis. We treated 9 consecutive patients with advanced-stage AL amyloidosis with single-agent elranatamab, observing a 100% overall response and 67% complete response rate, including minimal residual disease negativity, with expected toxicities. Median time to hematological response was 9 days (range, 6-24), with deep suppression in involved free light chains observed within 1 cycle of therapy, translating in cardiac and renal responses at 3 to 6 months. These data support prospective studies exploring elranatamab for patients with relapsed AL amyloidosis.

Article Details

Journal Blood
Volume / Issue Vol. 146, Issue 16
Published October 16, 2025
Pages 1929-1935
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (11)

P

Pedro Vianna

1Dana-Farber Cancer Institute, Jerome Lipper Multiple Myeloma Center, Department of Medical Oncology, Boston, United States

R

Rajshekhar Chakraborty

1Department of Medicine, Columbia University Irving Medical Center, New York, NY

S

Shahrier Hossain

1Dana-Farber Cancer Institute, Jerome Lipper Multiple Myeloma Center, Department of Medical Oncology, Boston, United States

D

Divaya Bhutani

Columbia University Medical Center, New York

S

Shannon Miller

A

Annemarie Rossi

2Department of Medical Oncology, Jerome Lipper Multiple Myeloma Center, Dana-Farber Cancer Institute, Boston, MA

S

Sarah A. M. Cuddy

3Harvard Medical School, Boston, MA

R

Rodney H. Falk

From the Department of Medicine, Northwestern Memorial Hospital, Chicago (C.W.Y.); and the Departments of Medicine (J.S.G., A.J.Y.), Radiology (B.G.G.), and Pathology (B.M.H.), Massachusetts General Hospital, the Departments of Medicine (J.S.G., R.H.F., A.J.Y.), Radiology (B.G.G.), and Pathology (B.M.H.), Harvard Medical School, and the Department of Medicine, Brigham and Women’s Hospital (R.H.F.) — all in Boston.

S

Suzanne Lentzsch

Columbia University Medical Center, New York, New York, United States

J

Jacob P. Laubach

G

Giada Bianchi