Risk factors and outcomes of asparaginase-associated pancreatitis in pediatric patients with ALL

C Changcheng Chen (1Department of Hematology/Oncology, Shanghai Children’s Medical Center, Shanghai Jiao Tong University School of Medicine, National Health Committee Key Laboratory of Pediatric Hematology and Oncology, Shanghai, China) J Jiaoyang Cai (1Department of Hematology/Oncology, Shanghai Children’s Medical Center, Shanghai Jiao Tong University School of Medicine, National Health Committee Key Laboratory of Pediatric Hematology and Oncology, Shanghai, China) X Xuedong Wu Q Qun Hu X Xiaoyan Wu X Xia Guo (Shenzhen Campus of Sun Yat-sen University) S Shaoyan Hu X Xiaowen Zhai (3Department of Hematology and Oncology, Children’s Hospital of Fudan University, Fudan University, Shanghai, China) B Benquan Qi (8Department of Pediatrics, State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Tianjin, China) W Weina Zhang (Guangdong-Hong Kong-Macao Joint Laboratory for Contaminants Exposure and Health, Guangdong Key Laboratory of Environmental Catalysis and Health Risk Control, Institute of Environmental Health and Pollution Control) N Ningling Wang (4Department of Pediatrics, The Second Affiliated Hospital of Anhui Medical University, Anhui Medical University, Hefei, China) F Fengling Xu (11Department of Hematology/Oncology, Chongqing Medical University Affiliated Children's Hospital, Chongqing, China) Y Yongjun Fang (12Department of Hematology/Oncology, Children's Hospital of Nanjing Medical University, Nanjing, China) C Chi-kong Li (13Department of Pediatrics, Hong Kong Children’s Hospital, The Chinese University of Hong Kong, Hong Kong SAR, China) C Changda Liang (14Department of Hematology/Oncology, Jiangxi Provincial Children's Hospital, Nanchang, China) L Lingzhen Wang J Jiashi Zhu (16Department of Hematology/Oncology, Children's Hospital Affiliated to Shanghai Jiao Tong University, Shanghai, China) W Wenjun Deng X Xin Tian (Wuya College of Innovation) X Xiuli Ju (13Department of Pediatrics, Qilu Hospital of Shandong University, Shandong University, Qingdao, China) G Ge Zhang J Jingyan Tang (State Key Laboratory of Molecular Engineering of Polymers) C Cheng Cheng J Jun Yang S Shuhong Shen (1Department of Hematology/Oncology, Shanghai Children’s Medical Center, Shanghai Jiao Tong University School of Medicine, National Health Committee Key Laboratory of Pediatric Hematology and Oncology, Shanghai, China) C Ching-Hon Pui

Abstract

Abstract Asparaginase-associated pancreatitis (AAP) is a significant complication in pediatric acute lymphoblastic leukemia (ALL) therapy, often leading to treatment delays or discontinuation. This study aimed to identify AAP risk factors, assess outcomes after first and second episodes, and evaluate the impact of asparaginase rechallenge. We retrospectively analyzed 7640 patients (aged 1 month to 18 years) treated under the Chinese Children Cancer Group ALL 2015 protocol. Patients were stratified as low risk (LR), intermediate risk (IR), or high risk (HR) based on clinical features and measurable residual disease (MRD). AAP was categorized as early or late onset depending on treatment phase. Older age and IR/HR status were independent risk factors for AAP. The cumulative AAP incidence was 2.2% in LR and 5.8% in IR/HR groups. Among 298 patients who developed AAP, 92 were rechallenged with asparaginase; second episodes occurred in 20.8% of LR and 33.8% of IR/HR patients, with no increase in severity. Lack of rechallenge and day 46 MRD of ≥0.01% were independently associated with inferior event-free survival (EFS). Among patients with early-onset AAP, those who were rechallenged had superior 5-year EFS than those who were not rechallenged (80.1% vs 60.2%; P = .003). Similarly, among IR/HR group, those who were rechallenged had better 5-year EFS than those who were not rechallenged (82.4% vs 60.6%; P = .004). IR/HR patients with early-onset AAP who were not rechallenged had especially poor outcomes (5-year EFS, 53.3%). These findings support considering asparaginase rechallenge in IR/HR patients with early-onset AAP when alternative therapies are limited. This trial was registered at www.chictr.org.cn as #ChiCTR2000032211.

Article Details

Journal Blood
Volume / Issue Vol. 146, Issue 20
Published November 13, 2025
Pages 2417-2427
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (26)

C

Changcheng Chen

1Department of Hematology/Oncology, Shanghai Children’s Medical Center, Shanghai Jiao Tong University School of Medicine, National Health Committee Key Laboratory of Pediatric Hematology and Oncology, Shanghai, China

J

Jiaoyang Cai

1Department of Hematology/Oncology, Shanghai Children’s Medical Center, Shanghai Jiao Tong University School of Medicine, National Health Committee Key Laboratory of Pediatric Hematology and Oncology, Shanghai, China

X

Xuedong Wu

Q

Qun Hu

X

Xiaoyan Wu

X

Xia Guo

Shenzhen Campus of Sun Yat-sen University

S

Shaoyan Hu

X

Xiaowen Zhai

3Department of Hematology and Oncology, Children’s Hospital of Fudan University, Fudan University, Shanghai, China

B

Benquan Qi

8Department of Pediatrics, State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Tianjin, China

W

Weina Zhang

Guangdong-Hong Kong-Macao Joint Laboratory for Contaminants Exposure and Health, Guangdong Key Laboratory of Environmental Catalysis and Health Risk Control, Institute of Environmental Health and Pollution Control

N

Ningling Wang

4Department of Pediatrics, The Second Affiliated Hospital of Anhui Medical University, Anhui Medical University, Hefei, China

F

Fengling Xu

11Department of Hematology/Oncology, Chongqing Medical University Affiliated Children's Hospital, Chongqing, China

Y

Yongjun Fang

12Department of Hematology/Oncology, Children's Hospital of Nanjing Medical University, Nanjing, China

C

Chi-kong Li

13Department of Pediatrics, Hong Kong Children’s Hospital, The Chinese University of Hong Kong, Hong Kong SAR, China

C

Changda Liang

14Department of Hematology/Oncology, Jiangxi Provincial Children's Hospital, Nanchang, China

L

Lingzhen Wang

J

Jiashi Zhu

16Department of Hematology/Oncology, Children's Hospital Affiliated to Shanghai Jiao Tong University, Shanghai, China

W

Wenjun Deng

X

Xin Tian

Wuya College of Innovation

X

Xiuli Ju

13Department of Pediatrics, Qilu Hospital of Shandong University, Shandong University, Qingdao, China

G

Ge Zhang

J

Jingyan Tang

State Key Laboratory of Molecular Engineering of Polymers

C

Cheng Cheng

J

Jun Yang

S

Shuhong Shen

1Department of Hematology/Oncology, Shanghai Children’s Medical Center, Shanghai Jiao Tong University School of Medicine, National Health Committee Key Laboratory of Pediatric Hematology and Oncology, Shanghai, China

C

Ching-Hon Pui