New England Journal of Medicine

Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy

R Richard S. Finkel (Center for Experimental Neurotherapeutics, Department of Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, TN) S Samuel H. Hughes (St. Jude Children’s Research Hospital, Memphis, TN) J JulieAnn Parker (OBGYN Partners of Augusta, Augusta, GA) M Matthew Civitello (St. Jude Children’s Research Hospital, Memphis, TN) A Alfonso Lavado H Heather C. Mefford L Lutz Mueller (F. Hoffmann–La Roche, Basel, Switzerland) H Heidemarie Kletzl (Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, Basel, Switzerland)
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Article Details

Volume / Issue Vol. 392, Issue 11
Published March 13, 2025
Pages 1138-1140
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society
ISSN: 0028-4793 Social Sciences

Authors (8)

R

Richard S. Finkel

Center for Experimental Neurotherapeutics, Department of Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, TN

S

Samuel H. Hughes

St. Jude Children’s Research Hospital, Memphis, TN

J

JulieAnn Parker

OBGYN Partners of Augusta, Augusta, GA

M

Matthew Civitello

St. Jude Children’s Research Hospital, Memphis, TN

A

Alfonso Lavado

H

Heather C. Mefford

L

Lutz Mueller

F. Hoffmann–La Roche, Basel, Switzerland

H

Heidemarie Kletzl

Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, Basel, Switzerland

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