Presymptomatic Treatment of a Genetic Disease with a Small-Molecule Drug
C
Charlotte J. Sumner
Article Details
Journal
New England Journal of Medicine
Volume / Issue
Vol. 393, Issue 7
Published
August 14, 2025
Pages
714-717
ISSN
0028-4793
Publisher
Massachusetts Medical Society
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
ISSN: 0028-4793 Social Sciences
Authors (1)
C
Charlotte J. Sumner
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