Phase 3 Trial of Oral Infigratinib in Children with Achondroplasia
Article Details
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
Authors (34)
Ravi Savarirayan
Murdoch Children’s Research Institute, Melbourne, VIC, Australia
Julie Hoover-Fong
Johns Hopkins University, Baltimore
Melita Irving
Guy’s and St. Thomas’ NHS Foundation Trust, London
Paul Arundel
Sheffield Children’s NHS Foundation Trust, Sheffield, United Kingdom
Josep Maria de Bergua
Arthroscopic Surgery Unit, Medical Innovation Knowledge Sharing Hospital, Vitoria-Gasteiz, Spain
Philippe M. Campeau
Toby Candler
University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, United Kingdom
Benjamin T. Cocanougher
Division of Human Genetics, Cincinnati Children’s Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati
Valérie Cormier-Daire
Thomas Edouard
Endocrine, Bone Diseases, and Genetics Unit, Reference Center for Rare Diseases of Calcium and Phosphate Metabolism, Pediatric Research Unit Centre d’Investigation Clinique 1436, Children’s Hospital, Toulouse University Hospital, Toulouse, France
Svein O. Fredwall
Oslo University Hospital, Oslo
Paul Harmatz
UCSF Benioff Children’s Hospital Oakland, Oakland, CA
Daniel Hoernschemeyer
University of Missouri, Columbia
Henrik U. Irgens
Haukeland University Hospital, Bergen, Norway
Saumya Jamuar
KK Women’s and Children’s Hospital, Singapore
Peter Kannu
University of Alberta–Stollery Children’s Hospital, Edmonton, Canada
Janet M. Legare
University of Wisconsin School of Medicine and Public Health, Madison
Antonio Leiva-Gea
Hospital Universitario Virgen de la Victoria, Instituto de Investigación Biomédica de Málaga, Plataforma Bionand, Hospital Quironsalud Málaga, and Department of Biomedicine, Faculty of Biomedical Sciences and Sports, Universidad Europea de Andalucía, Malaga, Spain
Helen McDevitt
NHS Greater Glasgow and Clyde, Glasgow, United Kingdom
Roberta Onesimo
Università Cattolica del Sacro Cuore–Fondazione Policlinico A. Gemelli IRCCS, Rome
John Phillips
Vanderbilt Health, Nashville
Mariana del Pino
Hospital de Pediatría Garrahan, Buenos Aires
Marie-Eve Robinson
Children’s Hospital of Eastern Ontario, University of Ottawa, Ottawa
Massimiliano Rossi
Hôpital Femme Mère Enfant, Hospices Civils de Lyon, Lyon, France
Mars Skae
Manchester University NHS Foundation Trust and University of Manchester, Manchester, United Kingdom
Leanne M. Ward
Children’s Hospital at London Health Sciences Centre, London, ON, Canada
Klane K. White
Children’s Hospital of Colorado, Aurora
Jane Schmidt
BridgeBio Pharma, San Francisco
Ted Lystig
BridgeBio Pharma, San Francisco
Ariana Salvatici
BridgeBio Pharma, San Francisco
Yun Bai
Institute of Energy Materials Science (IEMS)
Peter W. Butler
BridgeBio Pharma, San Francisco
David van Veenhuyzen
BridgeBio Pharma, San Francisco
Daniela Rogoff
BridgeBio Pharma, San Francisco