Phase 3 Trial of Oral Infigratinib in Children with Achondroplasia

R Ravi Savarirayan (Murdoch Children’s Research Institute, Melbourne, VIC, Australia) J Julie Hoover-Fong (Johns Hopkins University, Baltimore) M Melita Irving (Guy’s and St. Thomas’ NHS Foundation Trust, London) P Paul Arundel (Sheffield Children’s NHS Foundation Trust, Sheffield, United Kingdom) J Josep Maria de Bergua (Arthroscopic Surgery Unit, Medical Innovation Knowledge Sharing Hospital, Vitoria-Gasteiz, Spain) P Philippe M. Campeau T Toby Candler (University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, United Kingdom) B Benjamin T. Cocanougher (Division of Human Genetics, Cincinnati Children’s Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati) V Valérie Cormier-Daire T Thomas Edouard (Endocrine, Bone Diseases, and Genetics Unit, Reference Center for Rare Diseases of Calcium and Phosphate Metabolism, Pediatric Research Unit Centre d’Investigation Clinique 1436, Children’s Hospital, Toulouse University Hospital, Toulouse, France) S Svein O. Fredwall (Oslo University Hospital, Oslo) P Paul Harmatz (UCSF Benioff Children’s Hospital Oakland, Oakland, CA) D Daniel Hoernschemeyer (University of Missouri, Columbia) H Henrik U. Irgens (Haukeland University Hospital, Bergen, Norway) S Saumya Jamuar (KK Women’s and Children’s Hospital, Singapore) P Peter Kannu (University of Alberta–Stollery Children’s Hospital, Edmonton, Canada) J Janet M. Legare (University of Wisconsin School of Medicine and Public Health, Madison) A Antonio Leiva-Gea (Hospital Universitario Virgen de la Victoria, Instituto de Investigación Biomédica de Málaga, Plataforma Bionand, Hospital Quironsalud Málaga, and Department of Biomedicine, Faculty of Biomedical Sciences and Sports, Universidad Europea de Andalucía, Malaga, Spain) H Helen McDevitt (NHS Greater Glasgow and Clyde, Glasgow, United Kingdom) R Roberta Onesimo (Università Cattolica del Sacro Cuore–Fondazione Policlinico A. Gemelli IRCCS, Rome) J John Phillips (Vanderbilt Health, Nashville) M Mariana del Pino (Hospital de Pediatría Garrahan, Buenos Aires) M Marie-Eve Robinson (Children’s Hospital of Eastern Ontario, University of Ottawa, Ottawa) M Massimiliano Rossi (Hôpital Femme Mère Enfant, Hospices Civils de Lyon, Lyon, France) M Mars Skae (Manchester University NHS Foundation Trust and University of Manchester, Manchester, United Kingdom) L Leanne M. Ward (Children’s Hospital at London Health Sciences Centre, London, ON, Canada) K Klane K. White (Children’s Hospital of Colorado, Aurora) J Jane Schmidt (BridgeBio Pharma, San Francisco) T Ted Lystig (BridgeBio Pharma, San Francisco) A Ariana Salvatici (BridgeBio Pharma, San Francisco) Y Yun Bai (Institute of Energy Materials Science (IEMS)) P Peter W. Butler (BridgeBio Pharma, San Francisco) D David van Veenhuyzen (BridgeBio Pharma, San Francisco) D Daniela Rogoff (BridgeBio Pharma, San Francisco)

Article Details

Volume / Issue Vol. 1, Issue 1
Published June 28, 2026
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (34)

R

Ravi Savarirayan

Murdoch Children’s Research Institute, Melbourne, VIC, Australia

J

Julie Hoover-Fong

Johns Hopkins University, Baltimore

M

Melita Irving

Guy’s and St. Thomas’ NHS Foundation Trust, London

P

Paul Arundel

Sheffield Children’s NHS Foundation Trust, Sheffield, United Kingdom

J

Josep Maria de Bergua

Arthroscopic Surgery Unit, Medical Innovation Knowledge Sharing Hospital, Vitoria-Gasteiz, Spain

P

Philippe M. Campeau

T

Toby Candler

University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, United Kingdom

B

Benjamin T. Cocanougher

Division of Human Genetics, Cincinnati Children’s Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati

V

Valérie Cormier-Daire

T

Thomas Edouard

Endocrine, Bone Diseases, and Genetics Unit, Reference Center for Rare Diseases of Calcium and Phosphate Metabolism, Pediatric Research Unit Centre d’Investigation Clinique 1436, Children’s Hospital, Toulouse University Hospital, Toulouse, France

S

Svein O. Fredwall

Oslo University Hospital, Oslo

P

Paul Harmatz

UCSF Benioff Children’s Hospital Oakland, Oakland, CA

D

Daniel Hoernschemeyer

University of Missouri, Columbia

H

Henrik U. Irgens

Haukeland University Hospital, Bergen, Norway

S

Saumya Jamuar

KK Women’s and Children’s Hospital, Singapore

P

Peter Kannu

University of Alberta–Stollery Children’s Hospital, Edmonton, Canada

J

Janet M. Legare

University of Wisconsin School of Medicine and Public Health, Madison

A

Antonio Leiva-Gea

Hospital Universitario Virgen de la Victoria, Instituto de Investigación Biomédica de Málaga, Plataforma Bionand, Hospital Quironsalud Málaga, and Department of Biomedicine, Faculty of Biomedical Sciences and Sports, Universidad Europea de Andalucía, Malaga, Spain

H

Helen McDevitt

NHS Greater Glasgow and Clyde, Glasgow, United Kingdom

R

Roberta Onesimo

Università Cattolica del Sacro Cuore–Fondazione Policlinico A. Gemelli IRCCS, Rome

J

John Phillips

Vanderbilt Health, Nashville

M

Mariana del Pino

Hospital de Pediatría Garrahan, Buenos Aires

M

Marie-Eve Robinson

Children’s Hospital of Eastern Ontario, University of Ottawa, Ottawa

M

Massimiliano Rossi

Hôpital Femme Mère Enfant, Hospices Civils de Lyon, Lyon, France

M

Mars Skae

Manchester University NHS Foundation Trust and University of Manchester, Manchester, United Kingdom

L

Leanne M. Ward

Children’s Hospital at London Health Sciences Centre, London, ON, Canada

K

Klane K. White

Children’s Hospital of Colorado, Aurora

J

Jane Schmidt

BridgeBio Pharma, San Francisco

T

Ted Lystig

BridgeBio Pharma, San Francisco

A

Ariana Salvatici

BridgeBio Pharma, San Francisco

Y

Yun Bai

Institute of Energy Materials Science (IEMS)

P

Peter W. Butler

BridgeBio Pharma, San Francisco

D

David van Veenhuyzen

BridgeBio Pharma, San Francisco

D

Daniela Rogoff

BridgeBio Pharma, San Francisco