Phase 3 Trial of Inhaled Molgramostim in Autoimmune Pulmonary Alveolar Proteinosis

B Bruce C. Trapnell (Translational Pulmonary Science Center, Cincinnati Children’s Hospital Medical Center, Cincinnati) Y Yoshikazu Inoue (Clinical Research Center, National Hospital Organization Kinki-Chuo Chest Medical Center, Osaka, Japan) F Francesco Bonella (Center for Interstitial and Rare Lung Diseases, Pneumology Department, Ruhrlandklinik University Hospital, University of Duisburg–Essen, Essen, Germany) T Tisha Wang (Division of Pulmonary and Critical Care Medicine, University of California, Los Angeles, Los Angeles) C Cormac McCarthy (School of Medicine, University College Dublin, St. Vincent’s Hospital, Elm Park, Dublin) T Toru Arai (Clinical Research Center, National Hospital Organization Kinki-Chuo Chest Medical Center, Osaka, Japan) K Keiichi Akasaka (Department of Respiratory Medicine, Saitama Red Cross Hospital, Saitama, Japan) F Francesca Mariani (Pneumology Unit, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy) N Nesrin Mogulkoc (Department of Pulmonology, Ege University Hospital, Izmir, Turkey) J Jin Woo Song (Asan Medical Center, University of Ulsan College of Medicine, Seoul, South Korea) T Tomohisa Baba (Department of Respiratory Medicine, Kanagawa Cardiovascular and Respiratory Center, Kanagawa, Japan) S Stephane Jouneau (Centre Hospitalier Universitaire de Rennes, Hôpital Pontchaillou, Reference Center for Rare Pulmonary Diseases, Service de Pneumologie, Institut de Recherche en Santé, Environnement et Travail (Unité Mixte de Recherche 1085), Université de Rennes, Rennes, France) T Tadahisa Numakura (Department of Respiratory Medicine, Tohoku University Graduate School of Medicine, Sendai, Japan) N Nesrin Öcal (Health Sciences University, Gulhane Faculty of Medicine, Department of Pulmonology, Ankara, Turkey) F Florin Mihaltan A Ali Ataya (Division of Pulmonary, Critical Care and Sleep Medicine, Department of Medicine in the College of Medicine, University of Florida, Gainesville) E Elisabeth Bendstrup (Center for Rare Lung Diseases, Department of Respiratory Diseases and Allergy, Aarhus University Hospital, Aarhus, Denmark) I Ilaria Campo (Pneumology Unit, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy) B Brenna Carey (Translational Pulmonary Science Center, Cincinnati Children’s Hospital Medical Center, Cincinnati) R Ross Arena B Brian Robinson (Savara, Langhorne, PA) R Rosanna Fleming (Savara, Langhorne, PA) Y Yasmine Wasfi (Savara, Langhorne, PA) R Raymond Pratt (Savara, Langhorne, PA)

Article Details

Volume / Issue Vol. 393, Issue 8
Published August 21, 2025
Pages 764-773
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (24)

B

Bruce C. Trapnell

Translational Pulmonary Science Center, Cincinnati Children’s Hospital Medical Center, Cincinnati

Y

Yoshikazu Inoue

Clinical Research Center, National Hospital Organization Kinki-Chuo Chest Medical Center, Osaka, Japan

F

Francesco Bonella

Center for Interstitial and Rare Lung Diseases, Pneumology Department, Ruhrlandklinik University Hospital, University of Duisburg–Essen, Essen, Germany

T

Tisha Wang

Division of Pulmonary and Critical Care Medicine, University of California, Los Angeles, Los Angeles

C

Cormac McCarthy

School of Medicine, University College Dublin, St. Vincent’s Hospital, Elm Park, Dublin

T

Toru Arai

Clinical Research Center, National Hospital Organization Kinki-Chuo Chest Medical Center, Osaka, Japan

K

Keiichi Akasaka

Department of Respiratory Medicine, Saitama Red Cross Hospital, Saitama, Japan

F

Francesca Mariani

Pneumology Unit, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy

N

Nesrin Mogulkoc

Department of Pulmonology, Ege University Hospital, Izmir, Turkey

J

Jin Woo Song

Asan Medical Center, University of Ulsan College of Medicine, Seoul, South Korea

T

Tomohisa Baba

Department of Respiratory Medicine, Kanagawa Cardiovascular and Respiratory Center, Kanagawa, Japan

S

Stephane Jouneau

Centre Hospitalier Universitaire de Rennes, Hôpital Pontchaillou, Reference Center for Rare Pulmonary Diseases, Service de Pneumologie, Institut de Recherche en Santé, Environnement et Travail (Unité Mixte de Recherche 1085), Université de Rennes, Rennes, France

T

Tadahisa Numakura

Department of Respiratory Medicine, Tohoku University Graduate School of Medicine, Sendai, Japan

N

Nesrin Öcal

Health Sciences University, Gulhane Faculty of Medicine, Department of Pulmonology, Ankara, Turkey

F

Florin Mihaltan

A

Ali Ataya

Division of Pulmonary, Critical Care and Sleep Medicine, Department of Medicine in the College of Medicine, University of Florida, Gainesville

E

Elisabeth Bendstrup

Center for Rare Lung Diseases, Department of Respiratory Diseases and Allergy, Aarhus University Hospital, Aarhus, Denmark

I

Ilaria Campo

Pneumology Unit, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy

B

Brenna Carey

Translational Pulmonary Science Center, Cincinnati Children’s Hospital Medical Center, Cincinnati

R

Ross Arena

B

Brian Robinson

Savara, Langhorne, PA

R

Rosanna Fleming

Savara, Langhorne, PA

Y

Yasmine Wasfi

Savara, Langhorne, PA

R

Raymond Pratt

Savara, Langhorne, PA