Personalized Gene Editing to Treat an Inborn Error of Metabolism
A
Andrea L. Gropman
(Center for Experimental Neurotherapeutics, St. Jude Children’s Research Hospital, Memphis, TN)
A
Alexis C. Komor
(Department of Chemistry and Biochemistry, University of California, San Diego, La Jolla)
Article Details
Journal
New England Journal of Medicine
Volume / Issue
Vol. 392, Issue 22
Published
June 12, 2025
Pages
2273-2276
ISSN
0028-4793
Publisher
Massachusetts Medical Society
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
ISSN: 0028-4793 Social Sciences
Authors (2)
A
Andrea L. Gropman
Center for Experimental Neurotherapeutics, St. Jude Children’s Research Hospital, Memphis, TN
A
Alexis C. Komor
Department of Chemistry and Biochemistry, University of California, San Diego, La Jolla
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