PAM-flexible adenine base editing rescues hearing loss in a humanized MPZL2 mouse model harboring an East Asian founder mutation

S Shao Wei Hu S Sohyang Jeong L Luoying Jiang H Hansol Koo Z Zijing Wang W Won Hoon Choi B Biyun Zhu H Heeyoung Seok Y Yi Zhou M Min Gu Kim D Dan Mu H Huixia Guo Z Ziyi Zhou S Sung Ho Jung Y Yingting Zhang H Ho Byung Chae L Liheng Chen S Sung-Yeon Lee L Luo Guo M Myung-Whan Suh Y Yang Xiao M Moo Kyun Park H Honghai Tang J Jae-Jin Song X Xi Chen A Ai Chen J Jun Ho Lee (Department of Materials Science and Engineering) S Sangsu Bae S Sang-Yeon Lee Y Yilai Shu

Article Details

Volume / Issue Vol. 16, Issue 1
Published August 05, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (30)

S

Shao Wei Hu

S

Sohyang Jeong

L

Luoying Jiang

H

Hansol Koo

Z

Zijing Wang

W

Won Hoon Choi

B

Biyun Zhu

H

Heeyoung Seok

Y

Yi Zhou

M

Min Gu Kim

D

Dan Mu

H

Huixia Guo

Z

Ziyi Zhou

S

Sung Ho Jung

Y

Yingting Zhang

H

Ho Byung Chae

L

Liheng Chen

S

Sung-Yeon Lee

L

Luo Guo

M

Myung-Whan Suh

Y

Yang Xiao

M

Moo Kyun Park

H

Honghai Tang

J

Jae-Jin Song

X

Xi Chen

A

Ai Chen

J

Jun Ho Lee

Department of Materials Science and Engineering

S

Sangsu Bae

S

Sang-Yeon Lee

Y

Yilai Shu