Nickase NmCas9 unsilences paternal Ube3a in a mouse model of Angelman syndrome without causing AAV vector integration

H Hannah O. Bazick L Lucas M. James M Mark J. Zylka

Article Details

Volume / Issue Vol. 16, Issue 1
Published May 14, 2026
ISSN 2045-2322
Publisher Nature Portfolio

Journal Info

Scientific Reports

Nature Portfolio

ISSN: 2045-2322 Open Access Life Sciences

Authors (3)

H

Hannah O. Bazick

L

Lucas M. James

M

Mark J. Zylka