MRD-guided zanubrutinib, venetoclax, and obinutuzumab in relapsed CLL: primary end point analysis from the CLL2-BZAG trial

M Moritz Fürstenau (1Faculty of Medicine and University Hospital Cologne, Department I of Internal Medicine, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German CLL Study Group, University of Cologne, Cologne, Germany) S Sandra Robrecht (Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany) C Christof Schneider (Division of CLL, Department of Internal Medicine III, Ulm University, Ulm, Germany) E Eugen Tausch (Division of CLL, Department of Internal Medicine III, Ulm University, Ulm, Germany) A Adam Giza (1Faculty of Medicine and University Hospital Cologne, Department I of Internal Medicine, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German CLL Study Group, University of Cologne, Cologne, Germany) M Matthias Ritgen (Universitaetsklinikum Schleswig-Holstein, Medizinische Klinik II, Kiel, Germany) J Jörg Bittenbring (1José Carreras Center for Immuno- and Gene Therapy and Department of Internal Medicine I, Saarland University Medical School, Homburg, Germany) H Holger Hebart (2Kliniken Ostalb, Mutlangen, Germany) B Björn Schöttker (32Hämatologisch-Onkologische Schwerpunktpraxis Würzburg, Würzburg, Germany) A Anna Lena Illert U Ullrich Graeven A Andrea Stoltefuß (9Department of Hematology and Oncology, Evangelisches Krankenhaus Hamm, Hamm, Germany) B Bernhard Heinrich (10Hämatologisch-Onkologische Praxis Heinrich/Bangerter, Augsburg, Germany) R Robert Eckert (11Department of Hematology, Oncology, Stem Cell Transplantation, and Palliative Care, Klinikum Stuttgart, Katharinenhospital, Stuttgart, Germany) A Anna Fink J Janina Stumpf (Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany) K Kirsten Fischer (Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany) O Othman Al-Sawaf F Florian Simon (Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany) F Fanni Kleinert (1Department I of Internal Medicine, Faculty of Medicine and University Hospital Cologne, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German Chronic Lymphocytic Leukemia Study Group, University of Cologne, Cologne, Germany) J Jonathan Weiss (1Department I of Internal Medicine, Faculty of Medicine and University Hospital Cologne, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German Chronic Lymphocytic Leukemia Study Group, University of Cologne, Cologne, Germany) K Karl-Anton Kreuzer (Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany) A Anke Schilhabel (2University Hospital Schleswig-Holstein (UKSH) – Campus Kiel, Department of Hematology and Oncology, Kiel, Germany) M Monika Brüggemann (1Department of Internal Medicine II (Hematology/Oncology), University Hospital Schleswig-Holstein Campus Kiel, Kiel, Germany) P Petra Langerbeins (University Hospital, Cologne, Germany) S Stephan Stilgenbauer (Division of CLL, Department of Internal Medicine III, Ulm University, Ulm, Germany) B Barbara Eichhorst (Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany) M Michael Hallek (Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany) P Paula Cramer (18Department I of Internal Medicine, Faculty of Medicine and University Hospital of Cologne, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German Chronic Lymphocytic Leukemia Study Group, University of Cologne, Cologne, Germany)

Abstract

Abstract The phase 2 CLL2-BZAG trial tested a measurable residual disease (MRD)–guided combination treatment of zanubrutinib, venetoclax, and obinutuzumab after an optional bendamustine debulking in patients with relapsed/refractory chronic lymphocytic leukemia (CLL). In total, 42 patients were enrolled and 2 patients with ≤2 induction cycles were excluded from the analysis population per protocol. Patients had a median of 1 prior therapy (range, 1-5); 18 patients (45%) had already received a Bruton tyrosine kinase (BTK) inhibitor (BTKi); 7 patients (17.5%) venetoclax; and, of these, 5 (12.5%) had received both. Fifteen patients (37.5%) had a TP53 mutation/deletion, and 31 (77.5%) had unmutated immunoglobulin heavy chain variable region gene. With a median observation time of 21.5 months (range, 8.0-35.3) the most common adverse events were COVID-19 (n = 26 patients), diarrhea (n = 15), infusion-related reactions (n = 15), thrombocytopenia (n = 14), nausea (n = 12), fatigue (n = 12), and neutropenia (n = 12). Two patients had fatal adverse events (COVID-19, and fungal pneumonia secondary to COVID-19). After 6 months of the triple combination, all patients responded, and 21 (52.5%; 95% confidence interval, 36.1-68.5) showed undetectable MRD (uMRD) in the peripheral blood. In many patients, remissions deepened over time, with a best uMRD rate of 85%. The estimated progression-free and overall survival rates at 18 months were 96% and 96.8%, respectively. No patient has yet required a subsequent treatment. In summary, the MRD-guided triple combination of zanubrutinib, venetoclax, and obinutuzumab induced deep remissions in a relapsed CLL population enriched for patients previously treated with a BTKi/venetoclax. This trial was registered at www.clinicaltrials.gov as #NCT04515238.

Article Details

Journal Blood
Volume / Issue Vol. 145, Issue 12
Published March 20, 2025
Pages 1282-1292
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (29)

M

Moritz Fürstenau

1Faculty of Medicine and University Hospital Cologne, Department I of Internal Medicine, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German CLL Study Group, University of Cologne, Cologne, Germany

S

Sandra Robrecht

Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany

C

Christof Schneider

Division of CLL, Department of Internal Medicine III, Ulm University, Ulm, Germany

E

Eugen Tausch

Division of CLL, Department of Internal Medicine III, Ulm University, Ulm, Germany

A

Adam Giza

1Faculty of Medicine and University Hospital Cologne, Department I of Internal Medicine, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German CLL Study Group, University of Cologne, Cologne, Germany

M

Matthias Ritgen

Universitaetsklinikum Schleswig-Holstein, Medizinische Klinik II, Kiel, Germany

J

Jörg Bittenbring

1José Carreras Center for Immuno- and Gene Therapy and Department of Internal Medicine I, Saarland University Medical School, Homburg, Germany

H

Holger Hebart

2Kliniken Ostalb, Mutlangen, Germany

B

Björn Schöttker

32Hämatologisch-Onkologische Schwerpunktpraxis Würzburg, Würzburg, Germany

A

Anna Lena Illert

U

Ullrich Graeven

A

Andrea Stoltefuß

9Department of Hematology and Oncology, Evangelisches Krankenhaus Hamm, Hamm, Germany

B

Bernhard Heinrich

10Hämatologisch-Onkologische Praxis Heinrich/Bangerter, Augsburg, Germany

R

Robert Eckert

11Department of Hematology, Oncology, Stem Cell Transplantation, and Palliative Care, Klinikum Stuttgart, Katharinenhospital, Stuttgart, Germany

A

Anna Fink

J

Janina Stumpf

Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany

K

Kirsten Fischer

Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany

O

Othman Al-Sawaf

F

Florian Simon

Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany

F

Fanni Kleinert

1Department I of Internal Medicine, Faculty of Medicine and University Hospital Cologne, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German Chronic Lymphocytic Leukemia Study Group, University of Cologne, Cologne, Germany

J

Jonathan Weiss

1Department I of Internal Medicine, Faculty of Medicine and University Hospital Cologne, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German Chronic Lymphocytic Leukemia Study Group, University of Cologne, Cologne, Germany

K

Karl-Anton Kreuzer

Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany

A

Anke Schilhabel

2University Hospital Schleswig-Holstein (UKSH) – Campus Kiel, Department of Hematology and Oncology, Kiel, Germany

M

Monika Brüggemann

1Department of Internal Medicine II (Hematology/Oncology), University Hospital Schleswig-Holstein Campus Kiel, Kiel, Germany

P

Petra Langerbeins

University Hospital, Cologne, Germany

S

Stephan Stilgenbauer

Division of CLL, Department of Internal Medicine III, Ulm University, Ulm, Germany

B

Barbara Eichhorst

Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany

M

Michael Hallek

Department I of Internal Medicine, Center of Integrated Oncology Aachen Bonn Cologne Düsseldorf, University Hospital of Cologne, Cologne, Germany

P

Paula Cramer

18Department I of Internal Medicine, Faculty of Medicine and University Hospital of Cologne, Center for Integrated Oncology Aachen Bonn Cologne Duesseldorf, German Chronic Lymphocytic Leukemia Study Group, University of Cologne, Cologne, Germany