Morpholino–RNA duplex exhibits robust, sustained, and safe steric-block antisense activity by intracerebroventricular and intrathecal injection

M Mitsugu Yanagidaira T Tetsuya Nagata J Juri Hasegawa T Takashi Ishii S Satoe Ebihara M Makiko Nawa T Takanori Yokota

Article Details

Volume / Issue Vol. 16, Issue 1
Published December 22, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (7)

M

Mitsugu Yanagidaira

T

Tetsuya Nagata

J

Juri Hasegawa

T

Takashi Ishii

S

Satoe Ebihara

M

Makiko Nawa

T

Takanori Yokota