Lymphoid malignancies in patients with Shwachman-Diamond syndrome
Abstract
Abstract This study identified an increased risk of lymphoid malignancy in Shwachman-Diamond syndrome (SDS) with an observed risk 38-fold higher than expected based on population data. Increased toxicity was observed with standard therapies in patients with SDS.
Article Details
Authors (19)
Helen D. Reed
1Dana-Farber and Boston Children’s Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA
Hyunwoo Do
2Biostatistics and Research Design Center, Boston Children’s Hospital, Boston, MA
Edie Weller
3Boston Children's Hospital, Boston, United States
Marian H. Harris
Christopher R. Reilly
Harrison K. Tsai
4Department of Pathology, Boston Children’s Hospital, Boston, MA
Jason E. Farrar
6Arkansas Children’s Research Institute, Little Rock, AR
Bonnie W. Lau
8Department of Pediatrics, Dartmouth Health, Geisel School of Medicine at Dartmouth College, Lebanon, NH
Lauren Pommert
7Cincinnati Children's Hospital Medical Center, Division of Oncology, Cancer and Blood Diseases Institute, Cincinnati, United States
Christopher Gamper
11Johns Hopkins University School of Medicine, Baltimore, MD
Ian Atkinson
1Dana-Farber/Boston Children's Cancer and Blood Disorders Center; Harvard Medical School, Boston, United States
Katherine Coyne
1Dana-Farber and Boston Children’s Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA
Margret Joos
1Dana-Farber/Boston Children's Cancer and Blood Disorders Center; Harvard Medical School, Boston, United States
Sara Loveless
1Cincinnati Children's Hospital Medical Center, Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati, United States
Sarah Steltz
4Boston Children's Hospital, Clinical Research Center, Boston, United States
Leah Cheng
4Boston Children's Hospital, Clinical Research Center, Boston, United States
Maggie Malsch
1Dana-Farber/Boston Children's Cancer and Blood Disorders Center; Harvard Medical School, Boston, United States
Kasiani Myers
1Cincinnati Children's Hospital Medical Center, Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati, United States
Akiko Shimamura
Dana Farber/Boston Children's Cancer and Blood Disorders Center; Harvard Medical School, Boston, Massachusetts, United States