Lonvoguran Ziclumeran — In Vivo CRISPR Gene Editing in Hereditary Angioedema

D Danny M. Cohn (Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam) P Padmalal Gurugama (Cambridge University Hospitals, NHS Foundation Trust, Cambridge, United Kingdom) H Hilary J. Longhurst (Te Toka Tumai, Department of Immunology, Auckland City Hospital, Auckland, New Zealand) E Emel Aygören-Pürsün (Department of Children and Adolescents, University Hospital Frankfurt, Goethe University Frankfurt, Frankfurt, Germany) T Timothy J. Craig (Penn State University Departments of Medicine, Pediatrics, OB/GYN Maternal Fetal Medicine, and Biomedical Sciences, Hershey, PA) H Henriette Farkas (Hungarian Angioedema Center of Reference and Excellence, Department of Internal Medicine and Hematology, Semmelweis University, Budapest, Hungary) J Joshua Jacobs (Allergy and Asthma Clinical Research, Walnut Creek, CA) W William R. Lumry M Markus Magerl (Institute of Allergology, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin) J Jonny Peter (Division of Allergology and Clinical Immunology, Department of Medicine, Groote Schuur Hospital, University of Cape Town and Allergy and Immunology Unit, University of Cape Town Lung Institute, Cape Town, South Africa) M Marc A. Riedl (University of California, San Diego, La Jolla) D David Maag (Intellia Therapeutics, Cambridge, MA) A Adele Golden (Intellia Therapeutics, Cambridge, MA) M Mrinal Y. Shah (Intellia Therapeutics, Cambridge, MA) A Andrea Sutherland (Intellia Therapeutics, Cambridge, MA) C Catherine R. Miller (Intellia Therapeutics, Cambridge, MA) A Ahmed M. Abdelhady (Intellia Therapeutics, Cambridge, MA) Y Yuanxin Xu (Intellia Therapeutics, Cambridge, MA) J James S. Butler (Intellia Therapeutics, Cambridge, MA) D David Lebwohl (Intellia Therapeutics, Cambridge, MA) J John Leonard (Intellia Therapeutics, Cambridge, MA) A Aleena Banerji (Massachusetts General Hospital, Boston)

Article Details

Volume / Issue Vol. 1, Issue 1
Published June 12, 2026
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (22)

D

Danny M. Cohn

Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam

P

Padmalal Gurugama

Cambridge University Hospitals, NHS Foundation Trust, Cambridge, United Kingdom

H

Hilary J. Longhurst

Te Toka Tumai, Department of Immunology, Auckland City Hospital, Auckland, New Zealand

E

Emel Aygören-Pürsün

Department of Children and Adolescents, University Hospital Frankfurt, Goethe University Frankfurt, Frankfurt, Germany

T

Timothy J. Craig

Penn State University Departments of Medicine, Pediatrics, OB/GYN Maternal Fetal Medicine, and Biomedical Sciences, Hershey, PA

H

Henriette Farkas

Hungarian Angioedema Center of Reference and Excellence, Department of Internal Medicine and Hematology, Semmelweis University, Budapest, Hungary

J

Joshua Jacobs

Allergy and Asthma Clinical Research, Walnut Creek, CA

W

William R. Lumry

M

Markus Magerl

Institute of Allergology, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin

J

Jonny Peter

Division of Allergology and Clinical Immunology, Department of Medicine, Groote Schuur Hospital, University of Cape Town and Allergy and Immunology Unit, University of Cape Town Lung Institute, Cape Town, South Africa

M

Marc A. Riedl

University of California, San Diego, La Jolla

D

David Maag

Intellia Therapeutics, Cambridge, MA

A

Adele Golden

Intellia Therapeutics, Cambridge, MA

M

Mrinal Y. Shah

Intellia Therapeutics, Cambridge, MA

A

Andrea Sutherland

Intellia Therapeutics, Cambridge, MA

C

Catherine R. Miller

Intellia Therapeutics, Cambridge, MA

A

Ahmed M. Abdelhady

Intellia Therapeutics, Cambridge, MA

Y

Yuanxin Xu

Intellia Therapeutics, Cambridge, MA

J

James S. Butler

Intellia Therapeutics, Cambridge, MA

D

David Lebwohl

Intellia Therapeutics, Cambridge, MA

J

John Leonard

Intellia Therapeutics, Cambridge, MA

A

Aleena Banerji

Massachusetts General Hospital, Boston