Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1
Article Details
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
Authors (31)
Claire Booth
University College London Great Ormond Street Institute of Child Health, London
Julián Sevilla
Hematología y Hemoterapia, Fundación para la investigación Biomédica, Hospital Infantil Universitario Niño Jesús (HIUNJ), Madrid
Elena Almarza
Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER-ISCIII), Madrid
Caroline Y. Kuo
University of California, Los Angeles, Los Angeles
Josune Zubicaray
Hematología y Hemoterapia, Fundación para la investigación Biomédica, Hospital Infantil Universitario Niño Jesús (HIUNJ), Madrid
Dayna Terrazas
Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles
Grainne O’Toole
Department of Paediatric Immunology and Gene Therapy, Great Ormond Street Hospital for Sick Children NHS Foundation Trust, London
Maria Chitty-Lopez
Rocket Pharmaceuticals, Cranbury, NJ
Grace Choi
Rocket Pharmaceuticals, Cranbury, NJ
Eileen Nicoletti
Rocket Pharmaceuticals, Cranbury, NJ
Janel Long-Boyle
Department of Clinical Pharmacy, University of California, San Francisco, San Francisco
Augustine Fernandes
Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles
Kritika Chetty
University College London Great Ormond Street Institute of Child Health, London
Satiro De Oliveira
Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles
Crystal Banuelos
University of California, Los Angeles, Los Angeles
Jinhua Xu-Bayford
Department of Paediatric Immunology and Gene Therapy, Great Ormond Street Hospital for Sick Children NHS Foundation Trust, London
Antonella Lucía Bastone
Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany
Philipp John-Neek
Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany
Connie Jackson
University of California, Los Angeles, Los Angeles
Theodore B. Moore
Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles
Kimberly Gilmour
Great Ormond Street Hospital for Children NHS Trust, London
Axel Schambach
Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany
Michael Rothe
Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany
Sanchali Kasbekar
Rocket Pharmaceuticals, Cranbury, NJ
Gayatri R. Rao
Rocket Pharmaceuticals, Cranbury, NJ
Kinnari Patel
Rocket Pharmaceuticals, Cranbury, NJ
Gaurav Shah
Rocket Pharmaceuticals, Cranbury, NJ
Adrian J. Thrasher
University College London Great Ormond Street Institute of Child Health, London
Juan A. Bueren
Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER-ISCIII), Madrid
Jonathan D. Schwartz
Rocket Pharmaceuticals, Cranbury, NJ
Donald B. Kohn
Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles