IRF2 is an essential transcription factor with pathogenic and prognostic impact in multiple myeloma

N Nahia Gómez-Echarte (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) A Arantxa Carrasco-Leon A Alba Maiques-Diaz (Fundació de Recerca Clínic Barcelona-Institut d'Investigacions Biomèdiques August Pi Sunyer (FRCB-IDIBAPS), Spain) N Naroa Barrena (5Biomedical Engineering and Sciences Department, Tecnun School of Engineering, University of Navarra, San Sebastián, Spain) E Estibaliz Miranda (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) L Leire Garate (2Cancer Center Clínica Universidad de Navarra, Pamplona, Spain) A Ane Amundarain (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) P Patxi San Martín-Uriz (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) S Stella Charalampopoulou (4Fundació Clínic per la Recerca Biomèdica-Institut d’Investigacions Biomèdiques August Pi i Sunyer, Barcelona, Spain) L Luis Vitores Valcárcel (5Biomedical Engineering and Sciences Department, Tecnun School of Engineering, University of Navarra, San Sebastián, Spain) B Beñat Ariceta (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) P Paula Rodriguez-Marquez (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) J Juan Roberto Rodriguez-Madoz (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) K Kazuya Ishiguro (7Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA) F Francisco J. Planes (5Biomedical Engineering and Sciences Department, Tecnun School of Engineering, University of Navarra, San Sebastián, Spain) P Paula Rodriguez-Otero C Constantine S. Mitsiades (7Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA) J José Ignacio Martín-Subero E Edurne San José-Enériz (1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain) F Felipe Prosper X Xabier Agirre

Abstract

Abstract Multiple myeloma (MM), the second most prevalent hematologic malignancy, remains incurable, highlighting the need to identify molecular drivers of disease progression and new therapies. Using a CRISPR-Cas9 library screening approach in MM cells, we identified 22 essential transcription factors (TFs), including members of the interferon regulatory factor (IRF) family. Remarkably, in addition to the well-known IRF4, IRF2 emerged as a critical TF in MM. Cleavage under targets and release using nuclease (CUT&RUN) experiments demonstrated that IRF2 binds extensively to chromatin, both independently and in cooperation with IRF1 and IRF4. Although IRF2-unique regions were predominantly associated with active promoters, regions bound by IRF2/1/4 were biased toward introns. Functionally, IRF2 contributes to MM cell survival by suppressing necroptosis and promoting cell migration. Notably, IRF2-dependent transcriptional dysregulation was evident in precursor conditions such as monoclonal gammopathy of undetermined significance (MGUS) and smoldering MM (SMM), suggesting a role in early disease evolution. In addition to its role as an early factor, IRF2 levels also seem to influence disease progression, as MMs with higher expression demonstrated worse progression-free survival (PFS) and overall survival (OS) in both univariate and multivariate analyses, even after adjusting for common MM genetic risk factors. In conclusion, IRF2 constitutes an underappreciated essential TF involved in the pathogenesis and clinical behavior of MM. Its inhibition leads to dysregulation of key signaling pathways in MM pathogenesis, highlighting its potential as a therapeutic target.

Article Details

Journal Blood
Volume / Issue Vol. 147, Issue 26
Published June 25, 2026
Pages 3195-3208
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (21)

N

Nahia Gómez-Echarte

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

A

Arantxa Carrasco-Leon

A

Alba Maiques-Diaz

Fundació de Recerca Clínic Barcelona-Institut d'Investigacions Biomèdiques August Pi Sunyer (FRCB-IDIBAPS), Spain

N

Naroa Barrena

5Biomedical Engineering and Sciences Department, Tecnun School of Engineering, University of Navarra, San Sebastián, Spain

E

Estibaliz Miranda

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

L

Leire Garate

2Cancer Center Clínica Universidad de Navarra, Pamplona, Spain

A

Ane Amundarain

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

P

Patxi San Martín-Uriz

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

S

Stella Charalampopoulou

4Fundació Clínic per la Recerca Biomèdica-Institut d’Investigacions Biomèdiques August Pi i Sunyer, Barcelona, Spain

L

Luis Vitores Valcárcel

5Biomedical Engineering and Sciences Department, Tecnun School of Engineering, University of Navarra, San Sebastián, Spain

B

Beñat Ariceta

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

P

Paula Rodriguez-Marquez

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

J

Juan Roberto Rodriguez-Madoz

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

K

Kazuya Ishiguro

7Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA

F

Francisco J. Planes

5Biomedical Engineering and Sciences Department, Tecnun School of Engineering, University of Navarra, San Sebastián, Spain

P

Paula Rodriguez-Otero

C

Constantine S. Mitsiades

7Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA

J

José Ignacio Martín-Subero

E

Edurne San José-Enériz

1Center for Applied Medical Research, Universidad de Navarra, Navarra Medical Research Institute, Pamplona, Spain

F

Felipe Prosper

X

Xabier Agirre