Inability of α-cyclodextrins to accommodate cholesterol potentially underlies their lack of efficacy and ototoxicity in Niemann-Pick disease type C treatment

Y Yusei Yamada M Mayuko Tanaka Y Yusei Ikeda Y Yuki Kondo T Toru Takeo N Naomi Nakagata T Toru Miwa H Hiroki Takeda Y Yorihisa Orita K Keiichi Motoyama T Taishi Higashi H Hidetoshi Arima T Takahiro Seki Y Yuki Kurauchi H Hiroshi Katsuki K Katsumi Higaki K Kotaro Matsusaka K Kentaro Minami N Naoki Yoshikawa R Ryuji Ikeda M Muneaki Matsuo T Tetsumi Irie Y Yoichi Ishitsuka