In vivo mitochondrial base editing restores genotype and visual function in a mouse model of LHON

S Sanghun Kim J Jieun Kim (Neurosciences Preclinical Imaging Laboratory, Wu Tsai Neurosciences Institute, Stanford University, Stanford, CA, USA.) S Seongkwang Cha S Sungjin Ju C Chae Jin Lim S Seongho Hong J Jiyoung Bae Y Yeji Oh S Sungmo Jung S Sol Pin Kim H Hae-Sol Shin J Jae Hee Yoon J Jeeyoon Park S Seungmin Ryou S Soo-Yeon Lim S Su Bin Lee S Seung Hee Choi S Soo-ji Park C Chang Geun Choi M Mihyun Choi L Lark Kyun Kim J Jiyoon Park S Seonghyun Lee (School of Chemical and Biological Engineering and Institute of Chemical Process) K Kyoung Yul Seo J Je Kyung Seong K Kyoungmi Kim J Jin-Soo Kim H Hyunji Lee

Article Details

Volume / Issue Vol. 16, Issue 1
Published November 23, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (28)

S

Sanghun Kim

J

Jieun Kim

Neurosciences Preclinical Imaging Laboratory, Wu Tsai Neurosciences Institute, Stanford University, Stanford, CA, USA.

S

Seongkwang Cha

S

Sungjin Ju

C

Chae Jin Lim

S

Seongho Hong

J

Jiyoung Bae

Y

Yeji Oh

S

Sungmo Jung

S

Sol Pin Kim

H

Hae-Sol Shin

J

Jae Hee Yoon

J

Jeeyoon Park

S

Seungmin Ryou

S

Soo-Yeon Lim

S

Su Bin Lee

S

Seung Hee Choi

S

Soo-ji Park

C

Chang Geun Choi

M

Mihyun Choi

L

Lark Kyun Kim

J

Jiyoon Park

S

Seonghyun Lee

School of Chemical and Biological Engineering and Institute of Chemical Process

K

Kyoung Yul Seo

J

Je Kyung Seong

K

Kyoungmi Kim

J

Jin-Soo Kim

H

Hyunji Lee