In Vivo Base Editing of <i>PCSK9</i> with VERVE-102 for Hypercholesterolemia

S Scott B. Vafai (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) J Jörg Täubel (Richmond Pharmacology, London) T Thomas Ashdown (Richmond Pharmacology, London) R Riyaz S. Patel (Institute of Cardiovascular Science, University College London, London) S Sadaf Diamondali (Barts Health NHS Trust, London) J Jaimini Cegla (Imperial College London, London) H Handrean Soran (National Institute for Health and Care Research–Wellcome Trust Clinical Research Facility, Manchester University NHS Foundation Trust, Manchester, United Kingdom) B Bilal Bashir (National Institute for Health and Care Research–Wellcome Trust Clinical Research Facility, Manchester University NHS Foundation Trust, Manchester, United Kingdom) A Alexander Abitbol (LMC Diabetes and Endocrinology, Toronto) D Daniel Gaudet (Department of Medicine, Université de Montréal, Montreal) A Alex Lauzière (Department of Medicine, Université de Montréal, Montreal) L Liam R. Brunham (Department of Medicine, University of British Columbia, Vancouver, Canada) D David E. Newby (British Heart Foundation Centre for Research Excellence, University of Edinburgh, Edinburgh) S Stephen J. Nicholls (Victorian Heart Institute, Monash University, Melbourne, VIC, Australia) R Russell S. Scott (New Zealand Clinical Research, Christchurch, New Zealand) J Jane Kerr (New Zealand Clinical Research, Christchurch, New Zealand) J Jean-Claude Tardif (Montreal Heart Institute, Université de Montréal, Montreal) C Catherine Lunken (University College London Hospitals NHS Foundation Trust, London) S Steve E. Humphries (Institute of Cardiovascular Science, University College London, London) V Verena Karsten (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) P Patrick D. Tyler (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) X Xinyan Zhang (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) N Nidal Huniti (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) P Patrick A. Flight (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) C Chelsey L. Jensen (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) R Rick Falzone (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) J Joseph C. Biedenkapp (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) T Troy Lister (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) L Leslie E. Stolz (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) A Amit V. Khera (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston) S Sekar Kathiresan (Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston)

Article Details

Volume / Issue Vol. 1, Issue 1
Published May 25, 2026
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (31)

S

Scott B. Vafai

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

J

Jörg Täubel

Richmond Pharmacology, London

T

Thomas Ashdown

Richmond Pharmacology, London

R

Riyaz S. Patel

Institute of Cardiovascular Science, University College London, London

S

Sadaf Diamondali

Barts Health NHS Trust, London

J

Jaimini Cegla

Imperial College London, London

H

Handrean Soran

National Institute for Health and Care Research–Wellcome Trust Clinical Research Facility, Manchester University NHS Foundation Trust, Manchester, United Kingdom

B

Bilal Bashir

National Institute for Health and Care Research–Wellcome Trust Clinical Research Facility, Manchester University NHS Foundation Trust, Manchester, United Kingdom

A

Alexander Abitbol

LMC Diabetes and Endocrinology, Toronto

D

Daniel Gaudet

Department of Medicine, Université de Montréal, Montreal

A

Alex Lauzière

Department of Medicine, Université de Montréal, Montreal

L

Liam R. Brunham

Department of Medicine, University of British Columbia, Vancouver, Canada

D

David E. Newby

British Heart Foundation Centre for Research Excellence, University of Edinburgh, Edinburgh

S

Stephen J. Nicholls

Victorian Heart Institute, Monash University, Melbourne, VIC, Australia

R

Russell S. Scott

New Zealand Clinical Research, Christchurch, New Zealand

J

Jane Kerr

New Zealand Clinical Research, Christchurch, New Zealand

J

Jean-Claude Tardif

Montreal Heart Institute, Université de Montréal, Montreal

C

Catherine Lunken

University College London Hospitals NHS Foundation Trust, London

S

Steve E. Humphries

Institute of Cardiovascular Science, University College London, London

V

Verena Karsten

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

P

Patrick D. Tyler

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

X

Xinyan Zhang

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

N

Nidal Huniti

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

P

Patrick A. Flight

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

C

Chelsey L. Jensen

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

R

Rick Falzone

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

J

Joseph C. Biedenkapp

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

T

Troy Lister

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

L

Leslie E. Stolz

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

A

Amit V. Khera

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston

S

Sekar Kathiresan

Verve Therapeutics, a wholly owned subsidiary of Eli Lilly, Boston