IL-6 and ferritin levels predict the severity of cytopenia post CAR T-cell treatment with axi-cel for B cell lymphoma

A Alfadil Haroon (1Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) S Syed Ahmed R Reem Ahmad Awad (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) A Abdulwahab Albabtain (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) T Tamam Alshammari (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) R Riad El Fakih (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) T Tusneem Elhassan (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) A Alfadel Alshaibani (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) M Maha Elamin (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) D Dalal Alrifai (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) S Saud Alhayli (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) A Amal Aba Al Alaa (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) A Aml Hejab (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) N Naeem Chaudhri (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) M Maha Aljasser (1Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) A Abdulrhman Zaitoun (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) K Khalid Alsuhaibani (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) K Khaled Elshaer (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) A Abdullah Alamer (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) A Amer Abulathou (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) Z Zuheir Alkawi (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) F Farah Alhamdan (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) R Raghad Alrasheed (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) Y Yasmeen taha (3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia) F Fahad Almohareb (1King Faisal Specialist Hospital and Research Centre, Riyadh, Saudi Arabia) A Ali Alahmari W Walid Rasheed (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) H Hazza Alzahrani (2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia) M Mahmoud Aljurf

Abstract

Abstract Background: Chimeric Antigen Receptor (CAR) T-cell therapy is a promising treatment for hematologic malignancies such as B cell lymphomas but is associated with toxicities. Immune effector cell-associated hematotoxicity syndrome (ICAHT) which is serious but incompletely understood complication of CAR T-cell therapy. Understanding the incidence and risk factors for these adverse events remains essential for optimizing patient outcomes. Methods: A retrospective analysis of 85 patients with B cell lymphoma underwent Axi-cel CAR T-cell therapy was conducted. Patient demographics, overall survival (OS), incidence of ICANS, CRS, and cytopenias were evaluated. Risk factors for grade ≥3 cytopenias and prolonged cytopenias (>30 days) were assessed using univariate and multivariate logistic regression analyses. Results: The cohort included male 53 (63%) and female 32 (37.6%) patients with a median age of 53 (IQR:36 – 52) years. The 12-month OS was 75%. CRS was observed in 90.7% of patients, Grade 1 (28.2%), Grade 2 (35.9%), Grade 3 (23.1%), and Grade 4 (12.8%). Immune effector cell-associated neurotoxicity syndrome (ICANS) occurred in 83.7% of cases (Grade 1: 34.7%, Grade 2: 30.6%, Grade 3: 22.2%, Grade 4: 12.5%). Thrombocytopenia was reported in 62.8% of patients at different grades (Grade 1: 22.2%, Grade 2: 27.8%, Grade 3: 25.9%, Grade 4: 24.1%), while neutropenia was seen in 54.7% (Grade 1: 8.5%, Grade 2: 19.1%, Grade 3: 25.5%, Grade 4: 46.8%). Thrombocytopenia persisted for ≥30 days in 55.3% of cases and <30 days in 44.7%. Neutropenia lasted ≥30 days in 52.9% and <30 days in 47.1%. Anemia persists for ≥30 days was seen in 58.8% and <30 days in 41.2% of patients. Risk factors for grade 3-4 thrombocytopenia included pre Axi-cel infusion IL-6 >12 pg/mL (3-fold risk, P=0.026), ferritin >400 ng/mL (9-fold risk, P<0.001), time from last chemotherapy to lymphodepletion <45 days (5-fold risk, P=0.009), bone marrow involvement (2-fold risk, P=0.05), and pre-lymphodepletion thrombocytopenia (14-fold risk, P<0.001). Bridging radiation therapy was protective against neutropenia (0.4-fold risk, P=0.03). Prolonged cytopenias were associated with pre Axi-cel infusion IL-6 >12 pg/mL (4-fold risk for anemia, P=0.003), ferritin >400 ng/mL (2.5-fold risk for anemia, P=0.037; 4-fold risk for thrombocytopenia, P=0.008), time from last chemotherapy to lymphodepletion <45 days (P=0.04), and high LDH >400 (P=0.01 for anemia). In multivariate analysis, IL-6 was the only significant factor for anemia (OR=2.95, 95% CI 1.1-7.8, P=0.02), and ferritin was the only significant factor for prolonged thrombocytopenia (OR=3.5, 95% CI 1.3-9.8, P=0.01). For severe thrombocytopenia, significant factors included ferritin (OR=8.5, 95% CI 1.9-37.5, P=0.004), time from last chemotherapy to lymphodepletion <45 days (OR=0.23, 95% CI 0.06-0.9, P=0.03), and pre-lymphodepletion thrombocytopenia (OR=0.1, 95% CI 0.01-0.5, P=0.006). Conclusion: CAR T-cell therapy is associated with significant cytopenias, with IL-6 and ferritin levels as key predictors of anemia and thrombocytopenia, respectively. Pre-treatment factors such as recent chemotherapy and bone marrow involvement further increase the risk of cytopenias. These findings highlight the need for tailored monitoring and management strategies to mitigate hematologic toxicities in CAR T-cell therapy patients.

Article Details

Journal Blood
Volume / Issue Vol. 146, Issue Supplement 1
Published November 03, 2025
Pages 5495-5495
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (29)

A

Alfadil Haroon

1Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

S

Syed Ahmed

R

Reem Ahmad Awad

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

A

Abdulwahab Albabtain

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

T

Tamam Alshammari

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

R

Riad El Fakih

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

T

Tusneem Elhassan

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

A

Alfadel Alshaibani

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

M

Maha Elamin

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

D

Dalal Alrifai

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

S

Saud Alhayli

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

A

Amal Aba Al Alaa

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

A

Aml Hejab

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

N

Naeem Chaudhri

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

M

Maha Aljasser

1Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

A

Abdulrhman Zaitoun

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

K

Khalid Alsuhaibani

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

K

Khaled Elshaer

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

A

Abdullah Alamer

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

A

Amer Abulathou

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

Z

Zuheir Alkawi

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

F

Farah Alhamdan

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

R

Raghad Alrasheed

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

Y

Yasmeen taha

3Alfaisal University Faculty of Medicine, Riyadh, Saudi Arabia

F

Fahad Almohareb

1King Faisal Specialist Hospital and Research Centre, Riyadh, Saudi Arabia

A

Ali Alahmari

W

Walid Rasheed

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

H

Hazza Alzahrani

2Adult Hematology, stem cell transplant and cellular therapy section, Cancer Center of Excellence, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia

M

Mahmoud Aljurf