HNRNPC and m6A RNA methylation control oncogenic transcription and metabolism in T-cell leukemia

J Jonas De Kesel (1Ghent University, Ghent, Belgium) I Igor Fijalkowski (1Ghent University, Ghent, Belgium) T Tim Pieters (1Ghent University, Ghent, Belgium) C Cristina Borin (1Ghent University, Ghent, Belgium) K Kasper Thorhauge Christensen (1Ghent University, Ghent, Belgium) M Manou Wittouck (1Ghent University, Ghent, Belgium) J Jolien Van Laere (1Ghent University, Ghent, Belgium) L Laura Guerrero (Department of Bioengineering, Stanford University) L Lindy Reunes (1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium) M Marino Caruso (4Laboratory for Disease Mechanisms in Cancer, Department of Oncology, Katholieke Universiteit Leuven, Leuven, Belgium) B Bijal Thakkar (1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium) W Wouter Sleeckx L Luyao Kevin Xu (1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium) F Filip Van Nieuwerburgh D Dieter Deforce K Kim De Keersmaecker (4Laboratory for Disease Mechanisms in Cancer, Department of Oncology, Katholieke Universiteit Leuven, Leuven, Belgium) T Tim Lammens S Steven Goossens T Tom Taghon C Cuijuan Han (1The Jackson Laboratory, Farmington, United States) G Giulia Veltri (3University of Padova, Padova, Italy) V Valentina Serafin (4University of Modena and Reggio Emilia, Modena, Italy) B Bruno Palhais (1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium) N Nitesh D. Sharma (15Department of Pharmacology-Toxicology, University of Alabama at Birmingham, Birmingham, AL) H Hao Huang H Hudan Liu (16Department of Hematology, Zhongnan Hospital of Wuhan University, Wuhan, China) K Ksenia Matlawska-Wasowska (2University of Alabama at Birmingham, Birmingham, United States) A Ana Milovanovic (18Center for Genomic Regulation, The Barcelona Institute of Science and Technology, Barcelona, Spain) E Eva Maria Novoa E Eric Wang P Panagiotis Ntziachristos (1Ghent University, Ghent, Belgium)

Abstract

Abstract RNA homeostasis is dysregulated in cancer and affects disease progression and therapy resistance. N6-methyladenosine (m6A), the most abundant epitranscriptomic modification in eukaryotic messenger RNA, plays a pivotal role in RNA biology, affecting transcript stability, translation, and splicing. Our study uncovers the extensive m6A changes in patients with T-cell acute lymphoblastic leukemia (T-ALL), to our knowledge, for the first time. It reveals m6A’s regulatory role in the oncogenic MYC and cholesterol biosynthesis pathways. In addition, we discovered that T-ALL is highly dependent on the m6A reader heterogeneous nuclear ribonucleoprotein C (HNRNPC). HNRNPC is transcriptionally controlled by MYC and is an essential regulator of m6A-modified transcripts. Consequently, transcriptional silencing of HNRNPC profoundly impairs oncogenic pathways and critically diminishes leukemia cell growth. In addition, the levels of the m6A demethylase fat mass and obesity-associated protein (FTO) are significantly elevated in T-ALL cells compared with normal cells, and to other types of leukemia. Targeting FTO shows therapeutic potential in preclinical disease models and synergizes with clinically relevant therapeutics. Our findings underscore the integral role of RNA methylation in orchestrating cancer cell oncogene expression and metabolism and highlight promising novel therapeutic avenues for the treatment of T-cell leukemia.

Article Details

Journal Blood
Volume / Issue Vol. 146, Issue 3
Published July 17, 2025
Pages 275-290
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (31)

J

Jonas De Kesel

1Ghent University, Ghent, Belgium

I

Igor Fijalkowski

1Ghent University, Ghent, Belgium

T

Tim Pieters

1Ghent University, Ghent, Belgium

C

Cristina Borin

1Ghent University, Ghent, Belgium

K

Kasper Thorhauge Christensen

1Ghent University, Ghent, Belgium

M

Manou Wittouck

1Ghent University, Ghent, Belgium

J

Jolien Van Laere

1Ghent University, Ghent, Belgium

L

Laura Guerrero

Department of Bioengineering, Stanford University

L

Lindy Reunes

1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium

M

Marino Caruso

4Laboratory for Disease Mechanisms in Cancer, Department of Oncology, Katholieke Universiteit Leuven, Leuven, Belgium

B

Bijal Thakkar

1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium

W

Wouter Sleeckx

L

Luyao Kevin Xu

1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium

F

Filip Van Nieuwerburgh

D

Dieter Deforce

K

Kim De Keersmaecker

4Laboratory for Disease Mechanisms in Cancer, Department of Oncology, Katholieke Universiteit Leuven, Leuven, Belgium

T

Tim Lammens

S

Steven Goossens

T

Tom Taghon

C

Cuijuan Han

1The Jackson Laboratory, Farmington, United States

G

Giulia Veltri

3University of Padova, Padova, Italy

V

Valentina Serafin

4University of Modena and Reggio Emilia, Modena, Italy

B

Bruno Palhais

1Leukemia Therapy Resistance Lab, Department of Biomolecular Medicine, Faculty of Medicine and Health Sciences, Ghent University, Ghent, Belgium

N

Nitesh D. Sharma

15Department of Pharmacology-Toxicology, University of Alabama at Birmingham, Birmingham, AL

H

Hao Huang

H

Hudan Liu

16Department of Hematology, Zhongnan Hospital of Wuhan University, Wuhan, China

K

Ksenia Matlawska-Wasowska

2University of Alabama at Birmingham, Birmingham, United States

A

Ana Milovanovic

18Center for Genomic Regulation, The Barcelona Institute of Science and Technology, Barcelona, Spain

E

Eva Maria Novoa

E

Eric Wang

P

Panagiotis Ntziachristos

1Ghent University, Ghent, Belgium