Glucarpidase for treatment of high-dose methotrexate toxicity

S Shruti Gupta (Department of Anatomy and Cell Biology, The George Washington University) S Sarah A. Kaunfer (4Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) K Kevin L. Chen (4Department of Biostatistics, Harvard TH Chan School of Public Health, Boston, MA) J Julie-Alexia Dias (4Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) A Anitha Vijayan (5Division of Nephrology, Washington University School of Medicine, St. Louis, MO) A Arun Rajasekaran (7Division of Nephrology, Department of Medicine, University of Alabama at Birmingham, Birmingham, AL) J Jason M. Prosek (8Division of Nephrology, Department of Internal Medicine, The Ohio State University, Columbus, OH) H Huong L. Truong (9Department of Pharmacy, Mayo Clinic, Rochester, MN) A Anthony Wood (11Medical Oncology and Hematology, Arizona Center for Cancer Care, Phoenix, AZ) C Claude Bassil (13Department of Onco-Nephrology, H. Lee Moffitt Cancer Center and Research Institute, Tampa, FL) A Amanda D. Renaghan (14Division of Nephrology, University of Virginia Health System, Charlottesville, VA) C Chintan V. Shah (15Division of Nephrology, Hypertension, and Renal Transplant, Department of Medicine, University of Florida, Gainesville, FL) J Jingjing Zhang I Ilya Glezerman (17Renal Service, Memorial Sloan Kettering Cancer Center, New York, NY) C Christopher Carlos (19Division of Nephrology, Department of Medicine, University of California San Francisco, San Francisco, CA) K Katherine Kelly (20Department of Medicine, Indiana University School of Medicine, Indianapolis, IN) C Christopher J. Passero (21Renal-Electrolyte Division, Department of Medicine, University of Pittsburgh, Pittsburgh, PA) J Jan Drappatz (22Department of Neurology and Medicine, University of Pittsburgh, Pittsburgh, PA) A Ala Abudayyeh (23Division of Internal Medicine, Section of Nephrology, University of Texas MD Anderson Cancer Center, Houston, TX) D Daniel Sanghoon Shin (24Division of Hematology and Oncology, David Geffen School of Medicine at University of California Los Angeles, Los Angeles, CA) C C. John Sperati (25Division of Nephrology, Johns Hopkins University School of Medicine, Baltimore, MD) B Bradley J. Yelvington (26Department of Oncology Pharmacy, Vanderbilt University Medical Center, Nashville, TN) S Swetha R. Kanduri (27Department of Nephrology, Ochsner Health, New Orleans, LA) J Javier A. Neyra D Daniel Edmonston (29Division of Nephrology, Department of Medicine, Duke University School of Medicine, Durham, NC) A Anushree C. Shirali (30Section of Nephrology, Department of Internal Medicine, Yale University School of Medicine, New Haven, CT) A Anip Bansal (31Division of Renal Diseases and Hypertension, University of Colorado Anschutz Medical Campus, Aurora, CO) A Abdallah Geara (32Renal-Electrolyte and Hypertension Division, University of Pennsylvania, Philadelphia, PA) Z Zain Mithani S Susan L. Ziolkowski (34Division of Nephrology, Department of Medicine, Stanford University School of Medicine, Palo Alto, CA) A Arash Rashidi (35Division of Nephrology and Hypertension, University Hospitals Cleveland Medical Center, Cleveland, OH) J Jonathan Jakubowski (5Division of Nephrology, Washington University School of Medicine, St. Louis, MO) A Ashwini Pujari (7Division of Nephrology, Department of Medicine, University of Alabama at Birmingham, Birmingham, AL) D David A. Bond (36Division of Hematology, Department of Internal Medicine, Ohio State University Comprehensive Cancer Center, Columbus, OH) E Emily Dotson (37Department of Pharmacy, The Ohio State University, Columbus, OH) S Sarah Wall (2The Ohio State University Comprehensive Cancer Center - James Cancer Hospital, Columbus, United States) J John Patton (36Division of Hematology, Department of Internal Medicine, Ohio State University Comprehensive Cancer Center, Columbus, OH) J Jason N. Barreto (9Department of Pharmacy, Mayo Clinic, Rochester, MN) S Sandra M. Herrmann (38Division of Nephrology and Hypertension, Department of Internal Medicine, Mayo Clinic, Rochester, MN) M Mohammad S. Sheikh R Rachid Baz (1Department of Malignant Hematology, H. Lee Moffitt Cancer Center and Research Institute, Tampa, FL) J Jamie Lee (UCLA, Los Angeles, California, United States) N Nicholas Lucchesi (14Division of Nephrology, University of Virginia Health System, Charlottesville, VA) M Michael Kolman (15Division of Nephrology, Hypertension, and Renal Transplant, Department of Medicine, University of Florida, Gainesville, FL) M Muhammad Ahsan Rasheed (16Division of Nephrology, Department of Medicine, Thomas Jefferson University, Philadelphia, PA) A Afsheen Afzal (17Renal Service, Memorial Sloan Kettering Cancer Center, New York, NY) D Dasol Kang (17Renal Service, Memorial Sloan Kettering Cancer Center, New York, NY) A Amrita Mahesh (19Division of Nephrology, Department of Medicine, University of California San Francisco, San Francisco, CA) R Raymond K. Hsu (19Division of Nephrology, Department of Medicine, University of California San Francisco, San Francisco, CA) A Anthony Nicolaysen (40Division of Nephrology, Department of Medicine, University of California, Los Angeles, CA) K Kibrewessen Tefera (40Division of Nephrology, Department of Medicine, University of California, Los Angeles, CA) C Claire Schretlen (25Division of Nephrology, Johns Hopkins University School of Medicine, Baltimore, MD) R Ryan M. Miller (26Department of Oncology Pharmacy, Vanderbilt University Medical Center, Nashville, TN) J Juan Carlos Velez (27Department of Nephrology, Ochsner Health, New Orleans, LA) A Alexander H. Flannery (42Department of Pharmacy Practice and Science, University of Kentucky College of Pharmacy, Lexington, KY) A Abinet M. Aklilu (29Division of Nephrology, Department of Medicine, Duke University School of Medicine, Durham, NC) S Shuchi Anand (Division of Nephrology, Department of Medicine, Stanford University, Palo Alto, CA) S Soniya Chandrasekhara (44Department of Pharmacy, Stanford Healthcare, Stanford, CA) V Vicki Donley (35Division of Nephrology and Hypertension, University Hospitals Cleveland Medical Center, Cleveland, OH) A Ashka Patel J Jian Ni S Shobana Krishnamurthy (1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) R Rafia Ali (1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) O Osman A. Yilmam (1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) S Sophia L. Wells (1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) J Jessica L. Ortega (1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) O Olivia L. Green-Lingren (1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA) R Rebecca K. Leaf (Department of Medicine, Massachusetts General Hospital, Boston) M Meghan E. Sise (Department of Medicine, Massachusetts General Hospital, Boston) L Lakshmi Nayak (4Department of Medical Oncology, Center for Neuro Oncology, Dana Farber Cancer Institute, Boston, MA) A Ann S. LaCasce (3Harvard Medical School, Boston, MA) N Nelson Leung (1Mayo Clinic, Rochester, United States) D David E. Leaf (Division of Renal Medicine, Brigham and Women’s Hospital, Boston)

Abstract

Abstract High-dose methotrexate (MTX) results in high rates of acute kidney injury (AKI), neutropenia, and hepatotoxicity. Glucarpidase is a recombinant enzyme that cleaves MTX, but clinical data supporting its use are scarce. We examined the association between glucarpidase administration and outcomes in adults with MTX-AKI from 28 cancer centers across the United States using a sequential target trial emulation framework. The primary end point was kidney recovery at hospital discharge, defined as survival to discharge with serum creatinine <1.5-fold baseline and without dialysis dependence. Key secondary end points were time to kidney recovery, neutropenia, and transaminitis on day 7, and time to death. Using multivariable logistic and Cox regression models, we compared outcomes in patients who received glucarpidase within 4 days following MTX initiation with those in patients who did not. Among 708 patients with MTX-AKI, 209 (29.5%) received glucarpidase. Overall, 183 (25.8%) had a primary end point event. Glucarpidase receipt was associated with a 2.70-fold higher adjusted odds of kidney recovery (95% confidence interval [CI], 1.69–4.31) compared with no glucarpidase receipt. Patients treated with glucarpidase also had faster time to kidney recovery (adjusted hazard ratio [aHR], 1.88; 95% CI, 1.18–3.33) and lower risks of grade ≥2 neutropenia (adjusted odds ratio [aOR], 0.50; 95% CI, 0.28–0.91) and grade ≥2 transaminitis (aOR, 0.50; 95% CI, 0.28–0.91) on day 7. There was no difference in time to death (aHR, 0.76; 95% CI, 0.49–1.18). These data suggest glucarpidase may improve both renal and extrarenal outcomes in patients with MTX-AKI.

Article Details

Journal Blood
Volume / Issue Vol. 145, Issue 17
Published April 24, 2025
Pages 1858-1869
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (73)

S

Shruti Gupta

Department of Anatomy and Cell Biology, The George Washington University

S

Sarah A. Kaunfer

4Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

K

Kevin L. Chen

4Department of Biostatistics, Harvard TH Chan School of Public Health, Boston, MA

J

Julie-Alexia Dias

4Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

A

Anitha Vijayan

5Division of Nephrology, Washington University School of Medicine, St. Louis, MO

A

Arun Rajasekaran

7Division of Nephrology, Department of Medicine, University of Alabama at Birmingham, Birmingham, AL

J

Jason M. Prosek

8Division of Nephrology, Department of Internal Medicine, The Ohio State University, Columbus, OH

H

Huong L. Truong

9Department of Pharmacy, Mayo Clinic, Rochester, MN

A

Anthony Wood

11Medical Oncology and Hematology, Arizona Center for Cancer Care, Phoenix, AZ

C

Claude Bassil

13Department of Onco-Nephrology, H. Lee Moffitt Cancer Center and Research Institute, Tampa, FL

A

Amanda D. Renaghan

14Division of Nephrology, University of Virginia Health System, Charlottesville, VA

C

Chintan V. Shah

15Division of Nephrology, Hypertension, and Renal Transplant, Department of Medicine, University of Florida, Gainesville, FL

J

Jingjing Zhang

I

Ilya Glezerman

17Renal Service, Memorial Sloan Kettering Cancer Center, New York, NY

C

Christopher Carlos

19Division of Nephrology, Department of Medicine, University of California San Francisco, San Francisco, CA

K

Katherine Kelly

20Department of Medicine, Indiana University School of Medicine, Indianapolis, IN

C

Christopher J. Passero

21Renal-Electrolyte Division, Department of Medicine, University of Pittsburgh, Pittsburgh, PA

J

Jan Drappatz

22Department of Neurology and Medicine, University of Pittsburgh, Pittsburgh, PA

A

Ala Abudayyeh

23Division of Internal Medicine, Section of Nephrology, University of Texas MD Anderson Cancer Center, Houston, TX

D

Daniel Sanghoon Shin

24Division of Hematology and Oncology, David Geffen School of Medicine at University of California Los Angeles, Los Angeles, CA

C

C. John Sperati

25Division of Nephrology, Johns Hopkins University School of Medicine, Baltimore, MD

B

Bradley J. Yelvington

26Department of Oncology Pharmacy, Vanderbilt University Medical Center, Nashville, TN

S

Swetha R. Kanduri

27Department of Nephrology, Ochsner Health, New Orleans, LA

J

Javier A. Neyra

D

Daniel Edmonston

29Division of Nephrology, Department of Medicine, Duke University School of Medicine, Durham, NC

A

Anushree C. Shirali

30Section of Nephrology, Department of Internal Medicine, Yale University School of Medicine, New Haven, CT

A

Anip Bansal

31Division of Renal Diseases and Hypertension, University of Colorado Anschutz Medical Campus, Aurora, CO

A

Abdallah Geara

32Renal-Electrolyte and Hypertension Division, University of Pennsylvania, Philadelphia, PA

Z

Zain Mithani

S

Susan L. Ziolkowski

34Division of Nephrology, Department of Medicine, Stanford University School of Medicine, Palo Alto, CA

A

Arash Rashidi

35Division of Nephrology and Hypertension, University Hospitals Cleveland Medical Center, Cleveland, OH

J

Jonathan Jakubowski

5Division of Nephrology, Washington University School of Medicine, St. Louis, MO

A

Ashwini Pujari

7Division of Nephrology, Department of Medicine, University of Alabama at Birmingham, Birmingham, AL

D

David A. Bond

36Division of Hematology, Department of Internal Medicine, Ohio State University Comprehensive Cancer Center, Columbus, OH

E

Emily Dotson

37Department of Pharmacy, The Ohio State University, Columbus, OH

S

Sarah Wall

2The Ohio State University Comprehensive Cancer Center - James Cancer Hospital, Columbus, United States

J

John Patton

36Division of Hematology, Department of Internal Medicine, Ohio State University Comprehensive Cancer Center, Columbus, OH

J

Jason N. Barreto

9Department of Pharmacy, Mayo Clinic, Rochester, MN

S

Sandra M. Herrmann

38Division of Nephrology and Hypertension, Department of Internal Medicine, Mayo Clinic, Rochester, MN

M

Mohammad S. Sheikh

R

Rachid Baz

1Department of Malignant Hematology, H. Lee Moffitt Cancer Center and Research Institute, Tampa, FL

J

Jamie Lee

UCLA, Los Angeles, California, United States

N

Nicholas Lucchesi

14Division of Nephrology, University of Virginia Health System, Charlottesville, VA

M

Michael Kolman

15Division of Nephrology, Hypertension, and Renal Transplant, Department of Medicine, University of Florida, Gainesville, FL

M

Muhammad Ahsan Rasheed

16Division of Nephrology, Department of Medicine, Thomas Jefferson University, Philadelphia, PA

A

Afsheen Afzal

17Renal Service, Memorial Sloan Kettering Cancer Center, New York, NY

D

Dasol Kang

17Renal Service, Memorial Sloan Kettering Cancer Center, New York, NY

A

Amrita Mahesh

19Division of Nephrology, Department of Medicine, University of California San Francisco, San Francisco, CA

R

Raymond K. Hsu

19Division of Nephrology, Department of Medicine, University of California San Francisco, San Francisco, CA

A

Anthony Nicolaysen

40Division of Nephrology, Department of Medicine, University of California, Los Angeles, CA

K

Kibrewessen Tefera

40Division of Nephrology, Department of Medicine, University of California, Los Angeles, CA

C

Claire Schretlen

25Division of Nephrology, Johns Hopkins University School of Medicine, Baltimore, MD

R

Ryan M. Miller

26Department of Oncology Pharmacy, Vanderbilt University Medical Center, Nashville, TN

J

Juan Carlos Velez

27Department of Nephrology, Ochsner Health, New Orleans, LA

A

Alexander H. Flannery

42Department of Pharmacy Practice and Science, University of Kentucky College of Pharmacy, Lexington, KY

A

Abinet M. Aklilu

29Division of Nephrology, Department of Medicine, Duke University School of Medicine, Durham, NC

S

Shuchi Anand

Division of Nephrology, Department of Medicine, Stanford University, Palo Alto, CA

S

Soniya Chandrasekhara

44Department of Pharmacy, Stanford Healthcare, Stanford, CA

V

Vicki Donley

35Division of Nephrology and Hypertension, University Hospitals Cleveland Medical Center, Cleveland, OH

A

Ashka Patel

J

Jian Ni

S

Shobana Krishnamurthy

1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

R

Rafia Ali

1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

O

Osman A. Yilmam

1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

S

Sophia L. Wells

1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

J

Jessica L. Ortega

1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

O

Olivia L. Green-Lingren

1Division of Renal Medicine, Brigham and Women’s Hospital, Boston, MA

R

Rebecca K. Leaf

Department of Medicine, Massachusetts General Hospital, Boston

M

Meghan E. Sise

Department of Medicine, Massachusetts General Hospital, Boston

L

Lakshmi Nayak

4Department of Medical Oncology, Center for Neuro Oncology, Dana Farber Cancer Institute, Boston, MA

A

Ann S. LaCasce

3Harvard Medical School, Boston, MA

N

Nelson Leung

1Mayo Clinic, Rochester, United States

D

David E. Leaf

Division of Renal Medicine, Brigham and Women’s Hospital, Boston