Genome-wide association study of childhood B-cell acute lymphoblastic leukemia reveals novel African ancestry-specific susceptibility loci

C Cindy Im A Andrew R. Raduski L Lauren J. Mills K Kashi Raj Bhattarai R Robert J. Mobley K Kelly R. Barnett Z Zhanni Lu K Kenneth Liao N Nathan Anderson R Rebecca A. Johnson (McCourt School of Public Policy) E Erica Langer A Anthony J. Hooten A Alix E. Seif K Kathrin M. Bernt M Matthew Tsang B Brandon A. Mamou L Luis Gil-de-Gómez J Julie A. Wolfson D Danielle N. Friedman N Neerav Shukla L Laura J. Klesse E Erin L. Marcotte L Lingyun Ji A Alice Dang M Minjie Luo Y Yiming Zhong J Jalen Langie C Charleston W. K. Chiang A Adam de Smith J Joseph L. Wiemels A Andrew DeWan X Xiaomei Ma C Catherine Metayer Z Zhaoming Wang H Heather H. Nelson N Nathan Pankratz T Tianzhong Yang S Saonli Basu L Lucie M. Turcotte J Jun J. Yang (Department of Pharmacy and Pharmaceutical Sciences) D Daniel Savic M Michael E. Scheurer L Logan G. Spector

Abstract

Abstract B-cell acute lymphoblastic leukemia (B-ALL) is the most common pediatric malignancy. Given racial/ethnic differences in incidence and outcomes, B-ALL genome-wide association studies among children of African ancestry are needed. Leveraging multi-institutional datasets with 840 African American children with B-ALL and 3360 controls, nine loci achieved genome-wide significance ( P  < 5 × 10 −8 ) after meta-analysis. Two loci were established trans-ancestral susceptibility regions ( IKZF1 , ARID5B ), while the remaining novel loci were specific to African populations. Five-year overall survival among children carrying novel risk alleles was significantly worse (83% versus 96% in non-carriers, P  = 4.8 × 10 −3 ). Novel risk variants were also associated with subtype-specific disease ( P  < 0.05), including higher susceptibility for a subtype overrepresented in African American children ( TCF3-PBX1 ) and lower susceptibility for a subtype with excellent prognosis ( ETV6-RUNX1 ). Functional experiments revealed novel B-ALL risk variants had allele-specific differences in transcriptional activity ( P  < 0.05) in B-cell and leukemia cell lines. These findings shed insights into ancestry-related differences in leukemogenesis and prognosis.

Article Details

Volume / Issue Vol. 16, Issue 1
Published October 22, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (43)

C

Cindy Im

A

Andrew R. Raduski

L

Lauren J. Mills

K

Kashi Raj Bhattarai

R

Robert J. Mobley

K

Kelly R. Barnett

Z

Zhanni Lu

K

Kenneth Liao

N

Nathan Anderson

R

Rebecca A. Johnson

McCourt School of Public Policy

E

Erica Langer

A

Anthony J. Hooten

A

Alix E. Seif

K

Kathrin M. Bernt

M

Matthew Tsang

B

Brandon A. Mamou

L

Luis Gil-de-Gómez

J

Julie A. Wolfson

D

Danielle N. Friedman

N

Neerav Shukla

L

Laura J. Klesse

E

Erin L. Marcotte

L

Lingyun Ji

A

Alice Dang

M

Minjie Luo

Y

Yiming Zhong

J

Jalen Langie

C

Charleston W. K. Chiang

A

Adam de Smith

J

Joseph L. Wiemels

A

Andrew DeWan

X

Xiaomei Ma

C

Catherine Metayer

Z

Zhaoming Wang

H

Heather H. Nelson

N

Nathan Pankratz

T

Tianzhong Yang

S

Saonli Basu

L

Lucie M. Turcotte

J

Jun J. Yang

Department of Pharmacy and Pharmaceutical Sciences

D

Daniel Savic

M

Michael E. Scheurer

L

Logan G. Spector