Gene Therapy for Infantile-Onset Pompe’s Disease
G
Giancarlo Parenti
(Telethon Institute of Genetics and Medicine)
N
Nicola Brunetti-Pierri
Article Details
Journal
New England Journal of Medicine
Volume / Issue
Vol. 392, Issue 24
Published
June 26, 2025
Pages
2477-2478
ISSN
0028-4793
Publisher
Massachusetts Medical Society
Journal Info
New England Journal of Medicine
Massachusetts Medical Society
ISSN: 0028-4793 Social Sciences
Authors (2)
G
Giancarlo Parenti
Telethon Institute of Genetics and Medicine
N
Nicola Brunetti-Pierri
Related Articles from this Journal
Doctor’s Dirty Little Secret — The Cost of Silence
Tara Khan
Aug 2026
10.1056/nejmp2515506
Obstructive Hypertrophic Cardiomyopathy
Julian-Kai Nishizono, Marohito Nakata
Aug 2026
10.1056/nejmicm2603868
T-Cell Engager–Mediated HLA Antibody Depletion before Kidney Transplantation
Martina Schatzl, Katharina A. Mayer et al.
Jul 2026
10.1056/nejmc2603853
Products That Pose Health Risks — Can Litigation Protect Us When Government Fails?
Jerry Avorn
Jul 2026
10.1056/nejmp2604841
Precision Intensification in Metastatic Prostate Cancer
Rana R. McKay
Jul 2026
10.1056/nejme2605582