Exa-cel in Children with Transfusion-Dependent β-Thalassemia or Sickle Cell Disease

Haydar Frangoul

Sarah Cannon Research Institute at the Children’s Hospital at TriStar Centennial, Nashville

Josu de la Fuente

Imperial College Healthcare NHS Trust, St. Mary’s Hospital, London

Yogi Chopra

Hospital for Sick Children, Toronto

Roland Meisel

Division of Pediatric Stem Cell Therapy, Department of Pediatric Oncology, Hematology and Clinical Immunology, Medical Faculty, Heinrich-Heine-University, Düsseldorf, Germany

Persis J. Amrolia

Great Ormond Street Hospital for Children, London

Mattia Algeri

IRCCS Ospedale Pediatrico Bambino Gesù Rome, Rome

Akshay Sharma

Maria Domenica Cappellini

Unit of Medicine and Metabolic Disease, Fondazione IRCCS Ca’ Granda Ospedale Policlinico, Milan

Selim Corbacioglu

University of Regensburg, Regensburg, Germany

Antonis Kattamis

Stephan Lobitz

Gemeinschaftsklinikum Mittelrhein, Koblenz, Germany

Mariane De Montalembert

Damiano Rondelli

University of Illinois at Chicago, Chicago

Sujit Sheth

Joan and Sanford I Weill Medical College of Cornell University, New York

Martin H. Steinberg

Boston University Chobanian and Avedisian School of Medicine, Boston

Mark C. Walters

UCSF Benioff Children’s Hospital, Oakland, CA

Kevin Boerner

Vertex Pharmaceuticals, Boston

Tina Liu

Sakellarios Zairis

Vertex Pharmaceuticals, Boston

William Hobbs

Vertex Pharmaceuticals, Boston

Stephan A. Grupp

Franco Locatelli

IRCCS Ospedale Pediatrico Bambino Gesù Rome, Rome