Enhanced α2-3–linked sialylation determines the extended half-life of CHO-rVWF

C Ciara Byrne (1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) S Soracha Ward (1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) J Jamie O’Sullivan (1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) A Alain Chion (1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) P Patricia Lopes B Bogdan Baci (1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) C Caoimhe Dowd (1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) D Darragh Jordan (1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) R Ross Baker (1Perth Blood Institute, Perth, Australia) R Roger J. S. Preston M Marco Monopoli (4Department of Chemistry, Royal College of Surgeons in Ireland, Dublin, Ireland) P Peter L. Turecek (6Baxalta Innovations GmbH, a Member of the Takeda Group of Companies, Vienna, Austria) M Maximilianos Kotsias (6Ludger Ltd, Abingdon, United Kingdom) J Jack Cheeseman (6Ludger Ltd, Abingdon, United Kingdom) A Alan B. Moran R Richard A. Gardner (6Ludger Ltd, Abingdon, United Kingdom) D Daniel I. R. Spencer (6Ludger Ltd, Abingdon, United Kingdom) F Ferdows Atiq (2Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland) J James S. O’Donnell

Abstract

Abstract The half-life of recombinant human von Willebrand factor (rVWF) expressed in CHO cells (CHO-rVWF; Vonicog alfa; and Vonvendi/Veyvondi) is significantly longer than that of plasma-derived VWF (pdVWF). This finding is intriguing because CHO cells do not generate α2-6 sialylation, which constitutes the majority of human pdVWF sialylation. We hypothesized that glycan differences might regulate the longer half-life of CHO-rVWF. In lectin plate-binding assays and liquid chromatography–mass spectrometry analysis, we confirmed that CHO-rVWF lacked α2-6–linked sialylation. Conversely, however, α2-3–linked sialylation was significantly increased on CHO-rVWF, which also had reduced exposed β-galactose (β-Gal) compared to pdVWF. Consistent with human data, CHO-rVWF clearance was significantly (P < .001) reduced in VWF–/– mice compared to pdVWF. However, clearance of asialo-pdVWF and asialo–CHO-rVWF were identical. In keeping with the in vivo half-life prolongation, CHO-rVWF binding to murine macrophages (P = .012) and HepG2 cells (P = .001) was significantly decreased compared to pdVWF. Furthermore, CHO-rVWF binding to purified macrophage-galactose-type lectin (MGL) receptor and asialoglycoprotein receptor (ASGPR) was also significantly reduced. In contrast to pdVWF, in vivo studies in MGL1–/– mice and Asgr1–/– mice demonstrated that neither MGL nor ASGPR plays significant roles in regulating CHO-rVWF clearance. Together, our findings demonstrate that enhanced α2-3–linked sialylation on CHO-rVWF is responsible for its extended half-life.

Article Details

Journal Blood
Volume / Issue Vol. 145, Issue 23
Published June 05, 2025
Pages 2768-2773
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (19)

C

Ciara Byrne

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

S

Soracha Ward

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

J

Jamie O’Sullivan

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

A

Alain Chion

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

P

Patricia Lopes

B

Bogdan Baci

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

C

Caoimhe Dowd

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

D

Darragh Jordan

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

R

Ross Baker

1Perth Blood Institute, Perth, Australia

R

Roger J. S. Preston

M

Marco Monopoli

4Department of Chemistry, Royal College of Surgeons in Ireland, Dublin, Ireland

P

Peter L. Turecek

6Baxalta Innovations GmbH, a Member of the Takeda Group of Companies, Vienna, Austria

M

Maximilianos Kotsias

6Ludger Ltd, Abingdon, United Kingdom

J

Jack Cheeseman

6Ludger Ltd, Abingdon, United Kingdom

A

Alan B. Moran

R

Richard A. Gardner

6Ludger Ltd, Abingdon, United Kingdom

D

Daniel I. R. Spencer

6Ludger Ltd, Abingdon, United Kingdom

F

Ferdows Atiq

2Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland

J

James S. O’Donnell