Efficient mRNA delivery to resting T cells to reverse HIV latency

P Paula M. Cevaal S Stanislav Kan B Bridget M. Fisher M Michael A. Moso A Abigail Tan H Haiyin Liu A Abdalla Ali K Kiho Tanaka R Rory A. Shepherd Y Youry Kim J Jesslyn Ong D Denzil L. Furtado M Marvin Holz D Damian F. J. Purcell J Joshua M. L. Casan T Thomas Payne W Wei Zhao M Mohamed Fareh J James H. McMahon S Steven G. Deeks (Department of Medicine, University of California) R Rebecca Hoh (Department of Medicine, University of California) S Sushama Telwatte C Colin W. Pouton A Angus P. R. Johnston F Frank Caruso (Department of Chemical Engineering) J Jori Symons S Sharon R. Lewin (Department of Infectious Diseases, University of Melbourne, at the Peter Doherty Institute for Infection and Immunity) M Michael Roche

Abstract

Abstract A major hurdle to curing HIV is the persistence of integrated proviruses in resting CD4+ T cells that remain in a transcriptionally silent, latent state. One strategy to eradicate latent HIV is to activate viral transcription, followed by elimination of infected cells through virus-mediated cytotoxicity or immune-mediated clearance. We hypothesised that mRNA-lipid nanoparticle (LNP) technology would provide an opportunity to deliver mRNA encoding proteins able to reverse HIV latency in resting CD4+ T cells. Here we develop an LNP formulation (LNP X) with unprecedented potency to deliver mRNA to hard-to-transfect resting CD4+ T cells in the absence of cellular toxicity or activation. Encapsulating an mRNA encoding the HIV Tat protein, an activator of HIV transcription, LNP X enhances HIV transcription in ex vivo CD4+ T cells from people living with HIV. LNP X further enables the delivery of clustered regularly interspaced short palindromic repeats (CRISPR) activation machinery to modulate both viral and host gene transcription. These findings offer potential for the development of a range of nucleic acid-based T cell therapeutics.

Article Details

Volume / Issue Vol. 16, Issue 1
Published May 29, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (28)

P

Paula M. Cevaal

S

Stanislav Kan

B

Bridget M. Fisher

M

Michael A. Moso

A

Abigail Tan

H

Haiyin Liu

A

Abdalla Ali

K

Kiho Tanaka

R

Rory A. Shepherd

Y

Youry Kim

J

Jesslyn Ong

D

Denzil L. Furtado

M

Marvin Holz

D

Damian F. J. Purcell

J

Joshua M. L. Casan

T

Thomas Payne

W

Wei Zhao

M

Mohamed Fareh

J

James H. McMahon

S

Steven G. Deeks

Department of Medicine, University of California

R

Rebecca Hoh

Department of Medicine, University of California

S

Sushama Telwatte

C

Colin W. Pouton

A

Angus P. R. Johnston

F

Frank Caruso

Department of Chemical Engineering

J

Jori Symons

S

Sharon R. Lewin

Department of Infectious Diseases, University of Melbourne, at the Peter Doherty Institute for Infection and Immunity

M

Michael Roche