Efficacy and safety of givosiran in Japanese patients with acute hepatic porphyria: clinical findings from an expanded access study

N Nobuaki Ozaki Y Yoshie Goto N Norihisa Fujii T Takuro Oyama K Karen Frascello A Ana Camejo T Tomohide Adachi

Article Details

Volume / Issue Vol. 15, Issue 1
Published May 02, 2025
ISSN 2045-2322
Publisher Nature Portfolio

Journal Info

Scientific Reports

Nature Portfolio

ISSN: 2045-2322 Open Access Life Sciences

Authors (7)

N

Nobuaki Ozaki

Y

Yoshie Goto

N

Norihisa Fujii

T

Takuro Oyama

K

Karen Frascello

A

Ana Camejo

T

Tomohide Adachi