Early genetic evolution of driver mutations in uveal melanoma

J James J. Dollar C Christina L. Decatur E Ezekiel Weis A Amy C. Schefler M Miguel A. Materin T Timothy S. Fuller A Alison H. Skalet D David A. Reichstein I Ivana K. Kim K Kisha D. Piggott H Hakan Demirci T Thomas A. Aaberg P Prithvi Mruthyunjaya B Basil K. Williams E Eugene Shildkrot S Scott C. N. Oliver D Devron H. Char A Antonio Capone J John O. Mason S Scott D. Walter M Michael M. Altaweel J Jill R. Wells D Dan S. Gombos J Jay S. Duker P Peter G. Hovland T Tony Tsai C Cameron Javid M Michael A. Durante K Kyle R. Covington S Song Zhang Z Zelia M. Correa J J. William Harbour

Abstract

Abstract Uveal melanoma (UM) is an aggressive eye cancer that frequently results in metastatic death despite successful primary tumor treatment. Subclinical micrometastasis is thought to occur early, when tumors are small and difficult to distinguish from benign nevi. However, the early genetic evolution of UM is poorly understood, and biomarkers for malignant transformation are lacking. Here, we perform integrated genetic profiling of 1140 primary UMs, including 131 small tumors. A clinically available 15-gene expression profile (15-GEP) prospectively validated by our group is more accurate than driver mutations for predicting patient survival. Small tumors are significantly more likely to be in earlier stages of genetic evolution than larger tumors. Further, the 15-GEP support vector machine discriminant score predicts small tumors undergoing transformation from low-risk Class 1 to high-risk Class 2 profile. These results shed light on the early genetic evolution of UM and move us closer to a molecular definition of malignant transformation in this cancer type.

Article Details

Volume / Issue Vol. 16, Issue 1
Published December 12, 2025
ISSN 2041-1723
Publisher Nature Portfolio

Journal Info

Nature Communications

Nature Portfolio

ISSN: 2041-1723 Open Access Life Sciences

Authors (32)

J

James J. Dollar

C

Christina L. Decatur

E

Ezekiel Weis

A

Amy C. Schefler

M

Miguel A. Materin

T

Timothy S. Fuller

A

Alison H. Skalet

D

David A. Reichstein

I

Ivana K. Kim

K

Kisha D. Piggott

H

Hakan Demirci

T

Thomas A. Aaberg

P

Prithvi Mruthyunjaya

B

Basil K. Williams

E

Eugene Shildkrot

S

Scott C. N. Oliver

D

Devron H. Char

A

Antonio Capone

J

John O. Mason

S

Scott D. Walter

M

Michael M. Altaweel

J

Jill R. Wells

D

Dan S. Gombos

J

Jay S. Duker

P

Peter G. Hovland

T

Tony Tsai

C

Cameron Javid

M

Michael A. Durante

K

Kyle R. Covington

S

Song Zhang

Z

Zelia M. Correa

J

J. William Harbour