Dynamic monitoring of antibody drug conjugates targeting TROP2 or HER2 in breast cancer using circulating tumor cells

A Avanish Mishra (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) R Rachel O. Abelman (Division of Hematology Oncology, Massachusetts General Hospital Cancer Center and Department of Medicine, Harvard Medical School) Q Quinn Cunneely (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) V Victor Putaturo (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) A Akansha A. Deshpande (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) R Remy Bell (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) E Elizabeth M. Seider (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) K Katherine H. Xu (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) M Mythreayi Shan (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) J Justin Kelly (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) S Shih-Bo Huang (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) O Olivia Rieur (Division of Hematology Oncology, Massachusetts General Hospital Cancer Center and Department of Medicine, Harvard Medical School) J Justine Knape (Division of Hematology Oncology, Massachusetts General Hospital Cancer Center and Department of Medicine, Harvard Medical School) K Kaustav A. Gopinathan (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) K Kruthika Kikkeri (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) J Jon F. Edd (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) J John Walsh (Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School) C Charles S. Dai (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) L Leif W. Ellisen (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) D David T. Ting L Linda Nieman (Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School) M Mehmet Toner A Aditya Bardia D Daniel A. Haber S Shyamala Maheswaran

Abstract

Antibody–drug conjugates (ADCs) target surface proteins on cancer cells, leading to internalization and delivery of a drug payload, thereby enhancing selectivity and minimizing toxicity. ADCs against TROP2 (Sacituzumab govitecan) or HER2 (T-DXd) have demonstrated efficacy in metastatic breast cancer, yet paradoxically, outside of HER2 -amplified breast cancers, expression levels of these breast cancer-enriched epitopes in tumor biopsies have not been strongly correlated with clinical response. We undertook serial quantitative imaging of circulating tumor cells (CTCs) in a prospective cohort of 35 patients treated with either of these ADCs. At the single-cell level, expression of TROP2 and HER2 within individual patients is highly heterogeneous in both CTCs and paired tumor biopsies. Measurement of these epitopes on CTCs immediately prior to ADC therapy does not predict depth of clinical response. However, absence of CTCs or >80% reduction in CTC numbers after three weeks of treatment (CTC Low ) predicts durable response, compared with CTC High cases (TROP2: HR 5.15, P = 0.012; HER2: HR 6.01, P < 0.001). Targeted epitopes are not commonly downregulated on CTCs at the time of acquired clinical resistance, and switching between TROP2- and HER2-targeting ADCs sharing similar payloads infrequently leads to second-line response. Thus, while CTC burden is correlated with response to these ADCs, the level of TROP2 or HER2 expression is poorly predictive. These findings point to sensitivity to the drug payload as a potential driver of clinical response to currently approved ADCs in breast cancer.

Article Details

Volume / Issue Vol. 123, Issue 25
Published June 23, 2026
ISSN 0027-8424
Publisher National Academy of Sciences

Authors (25)

A

Avanish Mishra

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

R

Rachel O. Abelman

Division of Hematology Oncology, Massachusetts General Hospital Cancer Center and Department of Medicine, Harvard Medical School

Q

Quinn Cunneely

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

V

Victor Putaturo

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

A

Akansha A. Deshpande

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

R

Remy Bell

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

E

Elizabeth M. Seider

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

K

Katherine H. Xu

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

M

Mythreayi Shan

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

J

Justin Kelly

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

S

Shih-Bo Huang

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

O

Olivia Rieur

Division of Hematology Oncology, Massachusetts General Hospital Cancer Center and Department of Medicine, Harvard Medical School

J

Justine Knape

Division of Hematology Oncology, Massachusetts General Hospital Cancer Center and Department of Medicine, Harvard Medical School

K

Kaustav A. Gopinathan

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

K

Kruthika Kikkeri

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

J

Jon F. Edd

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

J

John Walsh

Center for Engineering in Medicine and Surgery, Massachusetts General Hospital and Harvard Medical School

C

Charles S. Dai

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

L

Leif W. Ellisen

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

D

David T. Ting

L

Linda Nieman

Krantz Family Center for Cancer Research, Massachusetts General Hospital Cancer Center and Harvard Medical School

M

Mehmet Toner

A

Aditya Bardia

D

Daniel A. Haber

S

Shyamala Maheswaran