DB-OTO Gene Therapy for Inherited Deafness

V Vassili Valayannopoulos (Regeneron Pharmaceuticals, Tarrytown, NY) M Manohar Bance D Daniela S. Carvalho (Department of Otolaryngology Head and Neck Surgery, University of California, San Diego, La Jolla) J John H. Greinwald (Cincinnati Children’s Hospital, University of Cincinnati, Cincinnati) S Steven A. Harvey (Department of Otolaryngology and Communication Sciences, Medical College of Wisconsin, Wauwatosa) A Akira Ishiyama (UCLA School of Medicine, Los Angeles) E Evie C. Landry (Nemours Children’s Health, Jacksonville, FL) H Hubert Löwenheim (Department of Otolaryngology–Head and Neck Surgery and Hearing Research Center, University of Tübingen Medical Center, Tübingen, Germany) L Lawrence R. Lustig (Department of Otolaryngology–Head and Neck Surgery, Columbia University Irving Medical Center, New York Presbyterian Hospital, New York) M Manuel Manrique (Otorhinolaryngology Department, University Clinic of Navarre, Pamplona, Spain) R Robert Nash (GOSH Institute of Child Health, University College London, London) R Rubén Polo (Head Otology and Lateral Skull Base Section, Ear, Nose, and Throat Department, Hospital Ramón y Cajal, Madrid) C Cedric V. Pritchett (Nemours Children’s Health, Orlando, FL) J Jay T. Rubinstein (Virginia Merrill Bloedel Hearing Research Center, Seattle Children’s Hospital, University of Washington, Seattle) A A. Eliot Shearer (Boston Children’s Hospital, Harvard Medical School, Boston) I Ignacio del Castillo (Servicio de Genética, Hospital Universitario Ramón y Cajal, Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Madrid) J Jeffery J. Anderson (Regeneron Pharmaceuticals, Tarrytown, NY) C C. Eduardo Corrales (Regeneron Pharmaceuticals, Tarrytown, NY) T Tera M. Quigley (Regeneron Pharmaceuticals, Tarrytown, NY) W William J. Riggs (Regeneron Pharmaceuticals, Tarrytown, NY) P Peter Weber (Regeneron Pharmaceuticals, Tarrytown, NY) G Gary Wilson (Regeneron Pharmaceuticals, Tarrytown, NY) S Susan C. Irvin (Regeneron Pharmaceuticals, Tarrytown, NY) H Hazem E. Hassan (Regeneron Pharmaceuticals, Tarrytown, NY) Y Yanping Chen R Rong Liu (School of Materials Science and Engineering) M Meghan C. Drummond (Regeneron Pharmaceuticals, Tarrytown, NY) L Leah R. Sabin (Regeneron Pharmaceuticals, Tarrytown, NY) B Bret J. Musser (Regeneron Pharmaceuticals, Tarrytown, NY) G George D. Yancopoulos (Regeneron Pharmaceuticals, Tarrytown, NY) C Christos A. Kyratsous G Gary A. Herman (Regeneron Pharmaceuticals, Tarrytown, NY) A Aris Baras J Jonathon P. Whitton (Regeneron Pharmaceuticals, Tarrytown, NY)

Article Details

Volume / Issue Vol. 394, Issue 11
Published March 12, 2026
Pages 1074-1083
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society

ISSN: 0028-4793 Social Sciences

Authors (34)

V

Vassili Valayannopoulos

Regeneron Pharmaceuticals, Tarrytown, NY

M

Manohar Bance

D

Daniela S. Carvalho

Department of Otolaryngology Head and Neck Surgery, University of California, San Diego, La Jolla

J

John H. Greinwald

Cincinnati Children’s Hospital, University of Cincinnati, Cincinnati

S

Steven A. Harvey

Department of Otolaryngology and Communication Sciences, Medical College of Wisconsin, Wauwatosa

A

Akira Ishiyama

UCLA School of Medicine, Los Angeles

E

Evie C. Landry

Nemours Children’s Health, Jacksonville, FL

H

Hubert Löwenheim

Department of Otolaryngology–Head and Neck Surgery and Hearing Research Center, University of Tübingen Medical Center, Tübingen, Germany

L

Lawrence R. Lustig

Department of Otolaryngology–Head and Neck Surgery, Columbia University Irving Medical Center, New York Presbyterian Hospital, New York

M

Manuel Manrique

Otorhinolaryngology Department, University Clinic of Navarre, Pamplona, Spain

R

Robert Nash

GOSH Institute of Child Health, University College London, London

R

Rubén Polo

Head Otology and Lateral Skull Base Section, Ear, Nose, and Throat Department, Hospital Ramón y Cajal, Madrid

C

Cedric V. Pritchett

Nemours Children’s Health, Orlando, FL

J

Jay T. Rubinstein

Virginia Merrill Bloedel Hearing Research Center, Seattle Children’s Hospital, University of Washington, Seattle

A

A. Eliot Shearer

Boston Children’s Hospital, Harvard Medical School, Boston

I

Ignacio del Castillo

Servicio de Genética, Hospital Universitario Ramón y Cajal, Instituto Ramón y Cajal de Investigación Sanitaria (IRYCIS), Madrid

J

Jeffery J. Anderson

Regeneron Pharmaceuticals, Tarrytown, NY

C

C. Eduardo Corrales

Regeneron Pharmaceuticals, Tarrytown, NY

T

Tera M. Quigley

Regeneron Pharmaceuticals, Tarrytown, NY

W

William J. Riggs

Regeneron Pharmaceuticals, Tarrytown, NY

P

Peter Weber

Regeneron Pharmaceuticals, Tarrytown, NY

G

Gary Wilson

Regeneron Pharmaceuticals, Tarrytown, NY

S

Susan C. Irvin

Regeneron Pharmaceuticals, Tarrytown, NY

H

Hazem E. Hassan

Regeneron Pharmaceuticals, Tarrytown, NY

Y

Yanping Chen

R

Rong Liu

School of Materials Science and Engineering

M

Meghan C. Drummond

Regeneron Pharmaceuticals, Tarrytown, NY

L

Leah R. Sabin

Regeneron Pharmaceuticals, Tarrytown, NY

B

Bret J. Musser

Regeneron Pharmaceuticals, Tarrytown, NY

G

George D. Yancopoulos

Regeneron Pharmaceuticals, Tarrytown, NY

C

Christos A. Kyratsous

G

Gary A. Herman

Regeneron Pharmaceuticals, Tarrytown, NY

A

Aris Baras

J

Jonathon P. Whitton

Regeneron Pharmaceuticals, Tarrytown, NY