Daratumumab-bortezomib-thalidomide-dexamethasone for newly diagnosed myeloma: CASSIOPEIA minimal residual disease results

J Jill Corre (Unité Génomique du Myélome, Hôpital Universitaire de Toulouse Oncopole, Université de Toulouse, Toulouse, France) L Laure Vincent (11Department of Hematology, Montpellier University Hospital, Montpellier, France) P Philippe Moreau B Benjamin Hebraud (2Institut Universitaire du Cancer, CHU Toulouse, Toulouse, France) C Cyrille Hulin (Service d’Hématologie, Hôpital Haut Lévêque, Centre Hospitalier Universitaire (CHU) de Bordeaux, Pessac, France) M Marie C. Béné (11Department of Hematology, Centre Hospitalier Universitaire de Nantes, Nantes, France) A Annemiek Broijl (1Department of Hematology, Erasmus MC Cancer Institute, Rotterdam, The Netherlands) D Denis Caillot (6Department of Hematology, Centre Hospitalier Universitaire Dijon, Hôpital Du Bocage, Dijon, France) M Michel Delforge T Thomas Dejoie (10Biochemistry Laboratory, Nantes University Hospital, Nantes, France) T Thierry Facon (6Department of Hematology, University Hospital and INSERM Unité Mixte de Recherche S1277, Lille, France) J Jérôme Lambert (Biostatistics and Medical Information Department, Hôpital St. Louis, Paris) X Xavier Leleu (Service Hématologie, Hôpital Universitaire de Poitiers, Poitiers, France) M Margaret Macro (Service Hématologie, Institut Hématologie de Basse Normandie, Hôpital Universitaire de Caen, Caen, France) A Aurore Perrot S Sonja Zweegman T Thomas Filleron (16Biostatistics and Health Data Science Unit, Oncopole Claudius Regaud, Institut Universitaire du Cancer Oncopole, Toulouse, France) B Bastien Cabarrou (16Biostatistics and Health Data Science Unit, Oncopole Claudius Regaud, Institut Universitaire du Cancer Oncopole, Toulouse, France) N Niels W. C. J. van de Donk S Sabrina Mahéo (IUCT, TOULOUSE, France) W Winnie Hua (17Cytel Inc, Waltham, MA) J Jianping Wang (Beijing National Laboratory for Molecular Sciences, College of Chemistry and Molecular Engineering) M Maria Krevvata (Johnson & Johnson, Spring House, PA) V Veronique Vanquickelberghe (Johnson & Johnson, Beerse, Belgium) C Carla de Boer (20Johnson & Johnson, Leiden, The Netherlands) A Alba Tuozzo (18Johnson & Johnson, Spring House, PA) F Fredrik Borgsten (21Johnson & Johnson, Raritan, NJ) M Melissa Rowe R Robin Carson (Johnson & Johnson, Spring House, PA) S Soraya Wuilleme (6Hematology Biology, University Hospital Hôtel-Dieu, Nantes, France) P Pieter Sonneveld

Abstract

Abstract Previous results from CASSIOPEIA demonstrated superior progression-free survival (PFS) and minimal residual disease (MRD) negativity with the addition of daratumumab to bortezomib, thalidomide, and dexamethasone (VTd) induction/consolidation and with daratumumab maintenance vs observation in transplant-eligible, newly diagnosed multiple myeloma. Here, we present long-term MRD status and PFS outcomes after a median follow-up of 80.1 months. Patients were randomly assigned (1:1) to daratumumab plus VTd (D-VTd) or VTd induction/consolidation; patients remaining on study were rerandomized to daratumumab maintenance or observation for ≤2 years. MRD status was assessed at predefined time points during each study phase. D-VTd improved overall MRD-negativity rates (10–5) after induction (34.6% vs 23.1%) and consolidation (63.7% vs 43.7%) and provided PFS benefit, regardless of postinduction MRD status, vs VTd alone. Daratumumab maintenance improved overall MRD-negativity rates over observation, regardless of induction/consolidation treatment (D-VTd/daratumumab vs D-VTd/observation, 10–5 [77.3% vs 70.7%] and 10–6 [60.7% vs 52.0%]; VTd/daratumumab vs VTd/observation, 10–5 [70.9% vs 51.2%] and 10–6 [48.4% vs 30.7%]) and improved MRD-negativity rates, regardless of risk status, as defined by cytogenetic abnormalities or the revised International Staging System score. Furthermore, daratumumab maintenance provided PFS benefit vs observation, regardless of induction/consolidation treatment and postconsolidation MRD status. D-VTd followed by daratumumab maintenance consistently produced the highest landmark, cumulative, and sustained MRD-negativity rates (10–5 and 10–6), translating to superior long-term PFS outcomes. These results demonstrate that daratumumab-based induction/consolidation followed by daratumumab maintenance resulted in the deepest and most durable MRD negativity, leading to superior PFS outcomes. This trial was registered at www.clinicaltrials.gov as #NCT02541383.

Article Details

Journal Blood
Volume / Issue Vol. 146, Issue 6
Published August 07, 2025
Pages 679-692
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (31)

J

Jill Corre

Unité Génomique du Myélome, Hôpital Universitaire de Toulouse Oncopole, Université de Toulouse, Toulouse, France

L

Laure Vincent

11Department of Hematology, Montpellier University Hospital, Montpellier, France

P

Philippe Moreau

B

Benjamin Hebraud

2Institut Universitaire du Cancer, CHU Toulouse, Toulouse, France

C

Cyrille Hulin

Service d’Hématologie, Hôpital Haut Lévêque, Centre Hospitalier Universitaire (CHU) de Bordeaux, Pessac, France

M

Marie C. Béné

11Department of Hematology, Centre Hospitalier Universitaire de Nantes, Nantes, France

A

Annemiek Broijl

1Department of Hematology, Erasmus MC Cancer Institute, Rotterdam, The Netherlands

D

Denis Caillot

6Department of Hematology, Centre Hospitalier Universitaire Dijon, Hôpital Du Bocage, Dijon, France

M

Michel Delforge

T

Thomas Dejoie

10Biochemistry Laboratory, Nantes University Hospital, Nantes, France

T

Thierry Facon

6Department of Hematology, University Hospital and INSERM Unité Mixte de Recherche S1277, Lille, France

J

Jérôme Lambert

Biostatistics and Medical Information Department, Hôpital St. Louis, Paris

X

Xavier Leleu

Service Hématologie, Hôpital Universitaire de Poitiers, Poitiers, France

M

Margaret Macro

Service Hématologie, Institut Hématologie de Basse Normandie, Hôpital Universitaire de Caen, Caen, France

A

Aurore Perrot

S

Sonja Zweegman

T

Thomas Filleron

16Biostatistics and Health Data Science Unit, Oncopole Claudius Regaud, Institut Universitaire du Cancer Oncopole, Toulouse, France

B

Bastien Cabarrou

16Biostatistics and Health Data Science Unit, Oncopole Claudius Regaud, Institut Universitaire du Cancer Oncopole, Toulouse, France

N

Niels W. C. J. van de Donk

S

Sabrina Mahéo

IUCT, TOULOUSE, France

W

Winnie Hua

17Cytel Inc, Waltham, MA

J

Jianping Wang

Beijing National Laboratory for Molecular Sciences, College of Chemistry and Molecular Engineering

M

Maria Krevvata

Johnson & Johnson, Spring House, PA

V

Veronique Vanquickelberghe

Johnson & Johnson, Beerse, Belgium

C

Carla de Boer

20Johnson & Johnson, Leiden, The Netherlands

A

Alba Tuozzo

18Johnson & Johnson, Spring House, PA

F

Fredrik Borgsten

21Johnson & Johnson, Raritan, NJ

M

Melissa Rowe

R

Robin Carson

Johnson & Johnson, Spring House, PA

S

Soraya Wuilleme

6Hematology Biology, University Hospital Hôtel-Dieu, Nantes, France

P

Pieter Sonneveld