New England Journal of Medicine

Cross-Correction in HSC Gene Therapy for Metachromatic Leukodystrophy

V Vasco Meneghini (IRCCS San Raffaele Scientific Institute, Milan) V Valeria Calbi (IRCCS San Raffaele Scientific Institute, Milan) F Filippo Casalini (IRCCS San Raffaele Scientific Institute, Milan) E Elisabeth Mangiameli (San Raffaele Telethon Institute for Gene Therapy, Milan) F Francesco Morena (Link Campus University, Rome) M Marco Piccoli (IRCCS Policlinico San Donato, San Donato Milanese, Italy) I Ilaria Laface (IRCCS San Raffaele Scientific Institute, Milan) I Ilaria Rossomanno (San Raffaele Telethon Institute for Gene Therapy, Milan) F Francesca Ornaghi (San Raffaele Telethon Institute for Gene Therapy, Milan) A Andrea Ghiroldi (IRCCS Policlinico San Donato, San Donato Milanese, Italy) P Paola M.V. Rancoita (Vita-Salute San Raffaele University, Milan) F Francesca Fumagalli (IRCCS San Raffaele Scientific Institute, Milan) S Sabata Martino (University of Perugia, Perugia, Italy) L Luigi Anastasia (Vita-Salute San Raffaele University, Milan) L Luigi Naldini A Alessandro Aiuti A Angela Gritti (San Raffaele Telethon Institute for Gene Therapy, Milan)
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Article Details

Volume / Issue Vol. 395, Issue 5
Published July 30, 2026
Pages 508-511
ISSN 0028-4793
Publisher Massachusetts Medical Society

Journal Info

New England Journal of Medicine

Massachusetts Medical Society
ISSN: 0028-4793 Social Sciences

Authors (17)

V

Vasco Meneghini

IRCCS San Raffaele Scientific Institute, Milan

V

Valeria Calbi

IRCCS San Raffaele Scientific Institute, Milan

F

Filippo Casalini

IRCCS San Raffaele Scientific Institute, Milan

E

Elisabeth Mangiameli

San Raffaele Telethon Institute for Gene Therapy, Milan

F

Francesco Morena

Link Campus University, Rome

M

Marco Piccoli

IRCCS Policlinico San Donato, San Donato Milanese, Italy

I

Ilaria Laface

IRCCS San Raffaele Scientific Institute, Milan

I

Ilaria Rossomanno

San Raffaele Telethon Institute for Gene Therapy, Milan

F

Francesca Ornaghi

San Raffaele Telethon Institute for Gene Therapy, Milan

A

Andrea Ghiroldi

IRCCS Policlinico San Donato, San Donato Milanese, Italy

P

Paola M.V. Rancoita

Vita-Salute San Raffaele University, Milan

F

Francesca Fumagalli

IRCCS San Raffaele Scientific Institute, Milan

S

Sabata Martino

University of Perugia, Perugia, Italy

L

Luigi Anastasia

Vita-Salute San Raffaele University, Milan

L

Luigi Naldini

A

Alessandro Aiuti

A

Angela Gritti

San Raffaele Telethon Institute for Gene Therapy, Milan

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