CRISPR activation for SCN2A-related neurodevelopmental disorders

S Serena Tamura A Andrew D. Nelson P Perry W. E. Spratt E Elizabeth C. Hamada X Xujia Zhou H Henry Kyoung Z Zizheng Li C Coline Arnould V Vladyslav Barskyi B Beniamin Krupkin K Kiana Young J Jingjing Zhao S Stephanie S. Holden A Atehsa Sahagun C Caroline M. Keeshen C Congyi Lu R Roy Ben-Shalom S Sunrae E. Taloma S Selin Schamiloglu Y Ying C. Li L Lia Min P Paul M. Jenkins J Jen Q. Pan J Jeanne T. Paz S Stephan J. Sanders N Navneet Matharu N Nadav Ahituv K Kevin J. Bender

Article Details

Journal Nature
Volume / Issue Vol. 646, Issue 8086
Published October 23, 2025
Pages 983-991
ISSN 0028-0836
Publisher Nature Portfolio

Journal Info

Nature

Nature Portfolio

ISSN: 0028-0836 Health Sciences

Authors (28)

S

Serena Tamura

A

Andrew D. Nelson

P

Perry W. E. Spratt

E

Elizabeth C. Hamada

X

Xujia Zhou

H

Henry Kyoung

Z

Zizheng Li

C

Coline Arnould

V

Vladyslav Barskyi

B

Beniamin Krupkin

K

Kiana Young

J

Jingjing Zhao

S

Stephanie S. Holden

A

Atehsa Sahagun

C

Caroline M. Keeshen

C

Congyi Lu

R

Roy Ben-Shalom

S

Sunrae E. Taloma

S

Selin Schamiloglu

Y

Ying C. Li

L

Lia Min

P

Paul M. Jenkins

J

Jen Q. Pan

J

Jeanne T. Paz

S

Stephan J. Sanders

N

Navneet Matharu

N

Nadav Ahituv

K

Kevin J. Bender