Common variation at 1q23.3, 2p23.3, 2q33.3, and 2p21 influences the risk of acute myeloid leukemia

D Diyanath Ranasinghe (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) W Wei-Yu Lin (Department of Medicinal and Applied Chemistry) S Sarah E. Fordham (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) A Abrar Alharbi (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) N Nicola J. Sunter (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) C Claire Elstob (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) M Mohammed H. Nahari (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) Y Yaobo Xu C Catherine Park E Eric Hungate (4University of Chicago Comprehensive Cancer Center, Chicago, IL) A Anne Quante (5Institute of Human Genetics, Technical University of Munich, TUM School of Medicine and Health, Klinikum rechts der Isar, TUM University Hospital, Munich, Germany) K Konstantin Strauch C Christian Gieger A Andrew Skol (4University of Chicago Comprehensive Cancer Center, Chicago, IL) T Thahira Rahman (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) L Lara Sucheston-Campbell (9Karmanos Cancer Institute and Department of Oncology, Wayne State University School of Medicine, Detroit, MI) T Theresa Hahn (10Department of Cancer Prevention, Roswell Park Cancer Institute, Buffalo, NY) A Alyssa I. Clay-Gilmour (11Department of Epidemiology and Biostatistics, Arnold School of Public Health, University of South Carolina, Columbia, SC) G Gail L. Jones (12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom) H Helen J. Marr (12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom) G Graham H. Jackson (12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom) T Tobias Menne (12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom) M Matthew Collin (Newcastle University, Newcastle Upon Tyne, United Kingdom) A Adam Ivey (6Alfred Hospital, Melbourne, VIC, Australia) R Robert K. Hills (14Nuffield Department of Population Health, University of Oxford, Oxford, United Kingdom) A Alan K. Burnett (15Paul O’Gorman Leukaemia Research Centre, University of Glasgow, Glasgow, United Kingdom) N Nigel H. Russell (Guy's and St Thomas' NHS Foundation Trust, London, United Kingdom) J Jude Fitzgibbon R Richard A. Larson M Michelle M. Le Beau (4University of Chicago Comprehensive Cancer Center, Chicago, IL) W Wendy Stock O Olaf Heidenreich (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) A Amir Enshaei D Dumni Gunasinghe (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) Z Zoë L. Hawking (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) H Holly Heslop (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) D Devi Nandana (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) B Bingjing Di (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) A Anna Plokhuta (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) I Imogen T. Brown (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) D David J. Allsup (20Centre for Biomedicine, Hull York Medical School, University of Hull, Hull, United Kingdom) R Richard S. Houlston A Andrew Collins (22School of Human Development and Health, Faculty of Medicine, University of Southampton, Southampton, United Kingdom) P Paul Milne (23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) J Jean Norden (23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) A Anne M. Dickinson (23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) C Clare Lendrem (23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) A Ann K. Daly (23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom) L Louise Palm (24West Midlands Regional Genetics Laboratory, Birmingham Women’s Hospital, Birmingham, United Kingdom) K Kim Piechocki (24West Midlands Regional Genetics Laboratory, Birmingham Women’s Hospital, Birmingham, United Kingdom) S Sally Jeffries (24West Midlands Regional Genetics Laboratory, Birmingham Women’s Hospital, Birmingham, United Kingdom) M Martin Bornhäuser C Christoph Röllig (22Department of Internal Medicine I, University Hospital TU Dresden, Dresden, Germany) H Heidi Altmann L Leo Ruhnke (27Medizinische Klinik und Poliklinik I, University Hospital Carl Gustav Carus Dresden, Technical University of Dresden, Dresden, Germany) D Desiree Kunadt (27Medizinische Klinik und Poliklinik I, University Hospital Carl Gustav Carus Dresden, Technical University of Dresden, Dresden, Germany) L Lisa Wagenführ (27Medizinische Klinik und Poliklinik I, University Hospital Carl Gustav Carus Dresden, Technical University of Dresden, Dresden, Germany) H Heather J. Cordell R Rebecca Darlay (28Population Health Sciences Institute, Newcastle University, Newcastle upon Tyne, United Kingdom) M Mette K. Andersen M Maria C. Fontana (30Institute of Hematology “L. and A. Seràgnoli,” University of Bologna, Bologna, Italy) G Giovanni Martinelli G Giovanni Marconi (31Hematology Unit, Ospedale S. Maria delle Croci, University of Bologna, Ravenna, Italy) M Miguel A. Sanz (32Hematology Service, Hospital Universitario y Politécnico La Fe, Valencia, Spain and CIBERONC, Instituto de Salud Carlos III, Madrid, Spain) J José Cervera (32Hematology Service, Hospital Universitario y Politécnico La Fe, Valencia, Spain and CIBERONC, Instituto de Salud Carlos III, Madrid, Spain) I Inés Gómez-Seguí (32Hematology Service, Hospital Universitario y Politécnico La Fe, Valencia, Spain and CIBERONC, Instituto de Salud Carlos III, Madrid, Spain) T Thomas Cluzeau (15Service d’Hématologie, Centre Hospitalier Universitaire de Nice, Nice, France) C Chimène Moreilhon (33CHU Pasteur, Service d’Hématologie Biologique, Université Côte d’Azur, Nice, France) S Sophie Raynaud (33CHU Pasteur, Service d’Hématologie Biologique, Université Côte d’Azur, Nice, France) H Heinz Sill (34Division of Hematology, Medical University of Graz, Graz, Austria) M Maria Teresa Voso H Hervé Dombret M Meyling Cheok (37Laboratory of Haematology, CHU Lille, Lille, France) C Claude Preudhomme (Unité Mixte de Recherche (UMR) 9020-UMR-S 1277-Canther-Cancer Heterogeneity, Plasticity and Resistance to Therapies, Institut de Recherche contre le Cancer de Lille, University of Lille, CNRS, Inserm, Centre Hospitalier Universitaire Lille, Lille, France) R Rosemary E. Gale (38Department of Haematology, University College London Cancer Institute, London, United Kingdom) D David Linch (38Department of Haematology, University College London Cancer Institute, London, United Kingdom) J Julia Weisinger (391st Department of Internal Medicine, Semmelweis University, Budapest, Hungary) A Andras Masszi (40Hematology and Lymphoma Unit, National Institute of Oncology, Budapest, Hungary) D Daniel Nowak W Wolf-Karsten Hofmann A Amanda Gilkes (42Department of Haematology, University of Cardiff, Cardiff, United Kingdom) K Kimmo Porkka (43Helsinki University Hospital Comprehensive Cancer Center, Hematology Research Unit Helsinki, University of Helsinki, Helsinki, Finland) J Jelena D. Milosevic Feenstra (44Department of Laboratory Medicine, Medical University of Vienna, Vienna, Austria) R Robert Kralovics (44Department of Laboratory Medicine, Medical University of Vienna, Vienna, Austria) J Junke Wang (State Key Laboratory for Flexible Electronics (LoFE)) M Manja Meggendorfer (46Munich Leukemia Laboratory, Munich, Germany) T Torsten Haferlach (7Munich Leukemia Laboratory, Munich, Germany) S Szilvia Krizsán (47MTA-SE Lendulet Molecular Oncohematology Research Group, Department of Pathology and Experimental Cancer Research, Semmelweis University, Budapest, Hungary) C Csaba Bödör B Brian Parkin (49Division of Hematology and Oncology, Department of Internal Medicine, University of Michigan, Ann Arbor, MI) S Sami N. Malek (Department of Internal Medicine, Division of Hematology and Oncology, University of Michigan) F Friedrich Stölzel (8Department of Internal Medicine II, Hematology and Oncology, University Medical Center Schleswig-Holstein, Campus Kiel, Kiel, Germany) K Kenan Onel J James M. Allan (1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom)

Abstract

Abstract Acute myeloid leukemia (AML) is a complex hematologic malignancy with multiple disease subgroups defined by somatic mutations and heterogeneous outcomes. Although genome-wide association studies (GWAS) have identified a small number of common genetic variants influencing AML risk, the heritable component of this disease outside of familial susceptibility remains largely undefined. Here, we perform a meta-analysis of 4 published GWAS plus 2 new GWAS, totaling 4710 AML cases and 12 938 controls. We identify a new genome-wide significant risk locus for pan-AML at 2p23.3 (rs4665765; P = 1.35 × 10−8; EFR3B, POMC, DNMT3A, and DNAJC27), which also significantly associates with patient survival (P = 6.09 × 10−3). Our analysis also identifies 3 new genome-wide significant risk loci for disease subgroups, including AML with deletions of chromosome 5 and/or 7 at 1q23.3 (rs12078864; P = 7.0 × 10−10; DUSP23) and cytogenetically complex AML at 2q33.3 (rs12988876; P = 3.28 × 10−8; PARD3B) and 2p21 (rs79918355; P = 1.60 × 10−9; EPCAM). We also investigated loci previously associated with the risk of clonal hematopoiesis (CH) or CH of indeterminate potential and identified several variants associated with the risk of AML. Our results further inform on AML etiology and demonstrate the existence of disease subgroup specific risk loci.

Article Details

Journal Blood
Volume / Issue Vol. 147, Issue 17
Published April 23, 2026
Pages 1958-1969
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (94)

D

Diyanath Ranasinghe

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

W

Wei-Yu Lin

Department of Medicinal and Applied Chemistry

S

Sarah E. Fordham

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

A

Abrar Alharbi

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

N

Nicola J. Sunter

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

C

Claire Elstob

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

M

Mohammed H. Nahari

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

Y

Yaobo Xu

C

Catherine Park

E

Eric Hungate

4University of Chicago Comprehensive Cancer Center, Chicago, IL

A

Anne Quante

5Institute of Human Genetics, Technical University of Munich, TUM School of Medicine and Health, Klinikum rechts der Isar, TUM University Hospital, Munich, Germany

K

Konstantin Strauch

C

Christian Gieger

A

Andrew Skol

4University of Chicago Comprehensive Cancer Center, Chicago, IL

T

Thahira Rahman

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

L

Lara Sucheston-Campbell

9Karmanos Cancer Institute and Department of Oncology, Wayne State University School of Medicine, Detroit, MI

T

Theresa Hahn

10Department of Cancer Prevention, Roswell Park Cancer Institute, Buffalo, NY

A

Alyssa I. Clay-Gilmour

11Department of Epidemiology and Biostatistics, Arnold School of Public Health, University of South Carolina, Columbia, SC

G

Gail L. Jones

12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom

H

Helen J. Marr

12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom

G

Graham H. Jackson

12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom

T

Tobias Menne

12Department of Haematology, Freeman Hospital, Newcastle upon Tyne Hospitals National Health Service Foundation Trust, Newcastle upon Tyne, United Kingdom

M

Matthew Collin

Newcastle University, Newcastle Upon Tyne, United Kingdom

A

Adam Ivey

6Alfred Hospital, Melbourne, VIC, Australia

R

Robert K. Hills

14Nuffield Department of Population Health, University of Oxford, Oxford, United Kingdom

A

Alan K. Burnett

15Paul O’Gorman Leukaemia Research Centre, University of Glasgow, Glasgow, United Kingdom

N

Nigel H. Russell

Guy's and St Thomas' NHS Foundation Trust, London, United Kingdom

J

Jude Fitzgibbon

R

Richard A. Larson

M

Michelle M. Le Beau

4University of Chicago Comprehensive Cancer Center, Chicago, IL

W

Wendy Stock

O

Olaf Heidenreich

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

A

Amir Enshaei

D

Dumni Gunasinghe

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

Z

Zoë L. Hawking

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

H

Holly Heslop

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

D

Devi Nandana

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

B

Bingjing Di

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

A

Anna Plokhuta

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

I

Imogen T. Brown

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

D

David J. Allsup

20Centre for Biomedicine, Hull York Medical School, University of Hull, Hull, United Kingdom

R

Richard S. Houlston

A

Andrew Collins

22School of Human Development and Health, Faculty of Medicine, University of Southampton, Southampton, United Kingdom

P

Paul Milne

23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

J

Jean Norden

23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

A

Anne M. Dickinson

23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

C

Clare Lendrem

23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

A

Ann K. Daly

23Translational and Clinical Research Institute, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom

L

Louise Palm

24West Midlands Regional Genetics Laboratory, Birmingham Women’s Hospital, Birmingham, United Kingdom

K

Kim Piechocki

24West Midlands Regional Genetics Laboratory, Birmingham Women’s Hospital, Birmingham, United Kingdom

S

Sally Jeffries

24West Midlands Regional Genetics Laboratory, Birmingham Women’s Hospital, Birmingham, United Kingdom

M

Martin Bornhäuser

C

Christoph Röllig

22Department of Internal Medicine I, University Hospital TU Dresden, Dresden, Germany

H

Heidi Altmann

L

Leo Ruhnke

27Medizinische Klinik und Poliklinik I, University Hospital Carl Gustav Carus Dresden, Technical University of Dresden, Dresden, Germany

D

Desiree Kunadt

27Medizinische Klinik und Poliklinik I, University Hospital Carl Gustav Carus Dresden, Technical University of Dresden, Dresden, Germany

L

Lisa Wagenführ

27Medizinische Klinik und Poliklinik I, University Hospital Carl Gustav Carus Dresden, Technical University of Dresden, Dresden, Germany

H

Heather J. Cordell

R

Rebecca Darlay

28Population Health Sciences Institute, Newcastle University, Newcastle upon Tyne, United Kingdom

M

Mette K. Andersen

M

Maria C. Fontana

30Institute of Hematology “L. and A. Seràgnoli,” University of Bologna, Bologna, Italy

G

Giovanni Martinelli

G

Giovanni Marconi

31Hematology Unit, Ospedale S. Maria delle Croci, University of Bologna, Ravenna, Italy

M

Miguel A. Sanz

32Hematology Service, Hospital Universitario y Politécnico La Fe, Valencia, Spain and CIBERONC, Instituto de Salud Carlos III, Madrid, Spain

J

José Cervera

32Hematology Service, Hospital Universitario y Politécnico La Fe, Valencia, Spain and CIBERONC, Instituto de Salud Carlos III, Madrid, Spain

I

Inés Gómez-Seguí

32Hematology Service, Hospital Universitario y Politécnico La Fe, Valencia, Spain and CIBERONC, Instituto de Salud Carlos III, Madrid, Spain

T

Thomas Cluzeau

15Service d’Hématologie, Centre Hospitalier Universitaire de Nice, Nice, France

C

Chimène Moreilhon

33CHU Pasteur, Service d’Hématologie Biologique, Université Côte d’Azur, Nice, France

S

Sophie Raynaud

33CHU Pasteur, Service d’Hématologie Biologique, Université Côte d’Azur, Nice, France

H

Heinz Sill

34Division of Hematology, Medical University of Graz, Graz, Austria

M

Maria Teresa Voso

H

Hervé Dombret

M

Meyling Cheok

37Laboratory of Haematology, CHU Lille, Lille, France

C

Claude Preudhomme

Unité Mixte de Recherche (UMR) 9020-UMR-S 1277-Canther-Cancer Heterogeneity, Plasticity and Resistance to Therapies, Institut de Recherche contre le Cancer de Lille, University of Lille, CNRS, Inserm, Centre Hospitalier Universitaire Lille, Lille, France

R

Rosemary E. Gale

38Department of Haematology, University College London Cancer Institute, London, United Kingdom

D

David Linch

38Department of Haematology, University College London Cancer Institute, London, United Kingdom

J

Julia Weisinger

391st Department of Internal Medicine, Semmelweis University, Budapest, Hungary

A

Andras Masszi

40Hematology and Lymphoma Unit, National Institute of Oncology, Budapest, Hungary

D

Daniel Nowak

W

Wolf-Karsten Hofmann

A

Amanda Gilkes

42Department of Haematology, University of Cardiff, Cardiff, United Kingdom

K

Kimmo Porkka

43Helsinki University Hospital Comprehensive Cancer Center, Hematology Research Unit Helsinki, University of Helsinki, Helsinki, Finland

J

Jelena D. Milosevic Feenstra

44Department of Laboratory Medicine, Medical University of Vienna, Vienna, Austria

R

Robert Kralovics

44Department of Laboratory Medicine, Medical University of Vienna, Vienna, Austria

J

Junke Wang

State Key Laboratory for Flexible Electronics (LoFE)

M

Manja Meggendorfer

46Munich Leukemia Laboratory, Munich, Germany

T

Torsten Haferlach

7Munich Leukemia Laboratory, Munich, Germany

S

Szilvia Krizsán

47MTA-SE Lendulet Molecular Oncohematology Research Group, Department of Pathology and Experimental Cancer Research, Semmelweis University, Budapest, Hungary

C

Csaba Bödör

B

Brian Parkin

49Division of Hematology and Oncology, Department of Internal Medicine, University of Michigan, Ann Arbor, MI

S

Sami N. Malek

Department of Internal Medicine, Division of Hematology and Oncology, University of Michigan

F

Friedrich Stölzel

8Department of Internal Medicine II, Hematology and Oncology, University Medical Center Schleswig-Holstein, Campus Kiel, Kiel, Germany

K

Kenan Onel

J

James M. Allan

1Translational and Clinical Research Institute, Newcastle University Centre for Cancer, Faculty of Medical Sciences, Newcastle University, Newcastle upon Tyne, United Kingdom