Common hereditary variants of the <i>APOE</i> gene and posttransplant outcome in acute myeloid leukemia

J Julian Ronnacker (1Department of Medicine A, University Hospital Münster, Münster, Germany) M Michael Grau (1Department of Medicine A, University Hospital Münster, Münster, Germany) M Maximilian Klasmeier (1Department of Medicine A, University Hospital Münster, Münster, Germany) C Christian Klesse (2Collaborative Biobank, DKMS Group gGmbH, Tübingen, Germany) H Henning Baldauf (15Clinical Trials Unit, DKMS Group, Tübingen und Dresden, Germany) S Stefan Abert (2Collaborative Biobank, DKMS Group gGmbH, Tübingen, Germany) A Andrew F. Berdel F Friederike T. Füsser (3Institute for Pharmaceutical and Medical Chemistry, University of Münster, Münster, Germany) S Sarah Sandmann J Jörn Albring (1Department of Medicine A, University Hospital Münster, Münster, Germany) C Christian Reicherts (1Department of Medicine A, Hematology, Oncology, and Pneumology, University Hospital Münster, Münster, Germany) S Simon Call (1University Hospital Muenster, Department of Medicine A, Hematology, Oncology and Pneumology, Muenster, Germany) J Julia Marx (1University Hospital Muenster, Department of Medicine A, Hematology, Oncology and Pneumology, Muenster, Germany) M Matthias Floeth (1Department of Medicine A, University Hospital Münster, Münster, Germany) E Eva Eßeling (19Department of Medicine A, Hematology, Oncology, and Respiratory Medicine, University Hospital Münster, Münster, Germany) L Lina Kolloch (1Department of Medicine A, University Hospital Münster, Münster, Germany) P Philipp Berning (1Human Oncology and Pathogenesis Program, Memorial Sloan Kettering Cancer Center, New York, United States) A Annika Scheller (1Department of Medicine A, University Hospital Münster, Münster, Germany) K Klaus Wethmar (27Department of Medicine A, Hematology, Oncology, Hemostaseology and Pneumology, University Hospital Münster, Münster, Germany) H Hartmut Schmidt (5Center for Laboratory Medicine, University Hospital Münster, Münster, Germany) B Bernhard Schlüter (5Center for Laboratory Medicine, University Hospital Münster, Münster, Germany) W Wolfgang E. Berdel B Benjamin N. Ostendorf (6Department of Hematology, Oncology, and Tumor Immunology, Berlin Institute of Health, Charité Universitätsmedizin Berlin, Berlin, Germany) S Sohail F. Tavazoie (8Laboratory of Systems Cancer Biology, The Rockefeller University, New York, NY) J Jan-Henrik Mikesch (1Department of Medicine A, Hematology, Oncology, and Pneumology, University Hospital Münster, Münster, Germany) G Georg Lenz K Katharina Fleischhauer (9Institute for Experimental Cellular Therapy, University Hospital Essen, Essen, Germany) J Johannes Schetelig (4Department of Internal Medicine I, University Hospital Dresden, Dresden University of Technology, Dresden, Germany) M Matthias Stelljes (16Department of Medicine A, University Hospital Münster, Münster, Germany) C Christoph Schliemann

Abstract

Abstract Apolipoprotein E (APOE) has multiple functions in metabolism and immunoregulation. Its common germ line variants APOE2, APOE3, and APOE4 give rise to 3 functionally distinct gene products. Previous studies reported yin-yang roles of APOE2 and APOE4 in immunological processes, but their effects in hematopoietic stem cell transplantation (HSCT) have never been studied. We performed APOE genotyping in 2 contemporary cohorts of 348 and 447 patients with acute myeloid leukemia who had received allogeneic HSCT and evaluated the associations of recipient and donor APOE genetic variations with posttransplant outcomes. Patients who carried at least 1 APOE2 allele had a higher risk of posttransplant death than APOE4 carriers in the discovery (hazard ratio [HR], 2.09; P = .024) and validation cohorts (HR, 1.96; P = .040). Detrimental APOE2 effects were driven by an increased risk of severe chronic graft-versus-host disease (GVHD; adjusted HR [HRadj], 1.85; P = .034) and nonrelapse death (HRadj, 1.72; P = .044). In non-APOE2 recipients, transplantation of an APOE2-positive allograft was associated with an increased incidence of grade 3 to 4 acute GVHD (HRadj, 2.82; P = .012) and severe chronic GVHD (HRadj, 2.54; P = .022) compared with APOE2-negative grafts. In summary, the APOE2 allele, typically considered a longevity gene in the general population, was associated with a higher risk of acute GVHD (HRadj, 2.75; P = .002), chronic GVHD (HRadj, 2.57; P = .001), and posttransplant mortality (HRadj, 1.79; P = .004), when present in either the host or transplanted from the donor.

Article Details

Journal Blood
Volume / Issue Vol. 145, Issue 17
Published April 24, 2025
Pages 1943-1956
ISSN 0006-4971
Publisher Elsevier BV

Journal Info

Blood

Elsevier BV

ISSN: 0006-4971 Health Sciences

Authors (30)

J

Julian Ronnacker

1Department of Medicine A, University Hospital Münster, Münster, Germany

M

Michael Grau

1Department of Medicine A, University Hospital Münster, Münster, Germany

M

Maximilian Klasmeier

1Department of Medicine A, University Hospital Münster, Münster, Germany

C

Christian Klesse

2Collaborative Biobank, DKMS Group gGmbH, Tübingen, Germany

H

Henning Baldauf

15Clinical Trials Unit, DKMS Group, Tübingen und Dresden, Germany

S

Stefan Abert

2Collaborative Biobank, DKMS Group gGmbH, Tübingen, Germany

A

Andrew F. Berdel

F

Friederike T. Füsser

3Institute for Pharmaceutical and Medical Chemistry, University of Münster, Münster, Germany

S

Sarah Sandmann

J

Jörn Albring

1Department of Medicine A, University Hospital Münster, Münster, Germany

C

Christian Reicherts

1Department of Medicine A, Hematology, Oncology, and Pneumology, University Hospital Münster, Münster, Germany

S

Simon Call

1University Hospital Muenster, Department of Medicine A, Hematology, Oncology and Pneumology, Muenster, Germany

J

Julia Marx

1University Hospital Muenster, Department of Medicine A, Hematology, Oncology and Pneumology, Muenster, Germany

M

Matthias Floeth

1Department of Medicine A, University Hospital Münster, Münster, Germany

E

Eva Eßeling

19Department of Medicine A, Hematology, Oncology, and Respiratory Medicine, University Hospital Münster, Münster, Germany

L

Lina Kolloch

1Department of Medicine A, University Hospital Münster, Münster, Germany

P

Philipp Berning

1Human Oncology and Pathogenesis Program, Memorial Sloan Kettering Cancer Center, New York, United States

A

Annika Scheller

1Department of Medicine A, University Hospital Münster, Münster, Germany

K

Klaus Wethmar

27Department of Medicine A, Hematology, Oncology, Hemostaseology and Pneumology, University Hospital Münster, Münster, Germany

H

Hartmut Schmidt

5Center for Laboratory Medicine, University Hospital Münster, Münster, Germany

B

Bernhard Schlüter

5Center for Laboratory Medicine, University Hospital Münster, Münster, Germany

W

Wolfgang E. Berdel

B

Benjamin N. Ostendorf

6Department of Hematology, Oncology, and Tumor Immunology, Berlin Institute of Health, Charité Universitätsmedizin Berlin, Berlin, Germany

S

Sohail F. Tavazoie

8Laboratory of Systems Cancer Biology, The Rockefeller University, New York, NY

J

Jan-Henrik Mikesch

1Department of Medicine A, Hematology, Oncology, and Pneumology, University Hospital Münster, Münster, Germany

G

Georg Lenz

K

Katharina Fleischhauer

9Institute for Experimental Cellular Therapy, University Hospital Essen, Essen, Germany

J

Johannes Schetelig

4Department of Internal Medicine I, University Hospital Dresden, Dresden University of Technology, Dresden, Germany

M

Matthias Stelljes

16Department of Medicine A, University Hospital Münster, Münster, Germany

C

Christoph Schliemann