Circulating protein biomarkers identified in two independent clinical trial cohorts of glucocorticoid-naive Duchenne muscular dystrophy patients.

F Fatemeh Ahmadiharchegani R Rebecca A. Tobin C Chiara Degan A Ahmed Naveed M Michela Guglieri A Albert Jiménez-Requena S Sharon I. de Vries C Cristina Al-Khalili Szigyarto P Pietro Spitali R Roula Tsonaka Y Yuri E. M. van der Burgt J Jordi Diaz-Manera J Jesse M. Damsker S Seth J. Perlman E Edward C. Smith I Iain Horrocks N Nicolas Deconinck N Nathalie M. Goemans J Jana Haberlova L Laurel Mengle-Gaw B Benjamin D. Schwartz A Amy Harper L Liesbeth De Waele D Diana Castro M Michele L. Yang M Monique M. Ryan E Erica Goude M Mar Tulinius R Richard I. Webster N Nancy Kuntz V Vamshi K. Rao A Annie M. Sbrocchi K Kathryn A. Selby M Migvis Monduy Y Yoram Nevo J Juan J. Vilchez A Andres Nascimento-Osorio E Erik H. Niks I Imelda JM De Groot M Marina Katsalouli J John N. Van DenAnker L Leanne M. Ward (Children’s Hospital at London Health Sciences Centre, London, ON, Canada) M Mika Leinonen T Tina Duong C Carolina Tesi Rocha M MD Andrea L. D’Alessandro L Lauren P. Morgenroth K Kate Bushby M Michael P. McDermott K Kimberly A. Hart R Rabi Tawil W William B. Martens B Barbara E. Herr E Elaine McColl C Chris Speed J Jennifer Wilkinson J Janbernd Kirschner W Wendy M. King M Michelle Eagle M Mary W. Brown T Tracey Willis R Robert C. Griggs V Volker Straub H Henriette van Ruiten A Anne-Marie Childs E Emma Ciafaloni (University of Rochester, Rochester, NY) P Perry B. Shieh S Stefan Spinty L Lorenzo Maggi G Giovanni Baranello R Russell J. Butterfield I IA Horrocks H Helen Roper Z Zoya Alhaswani K Kevin M. Flanigan (Nationwide Children’s Hospital, Columbus, OH) N Nancy L. Kuntz A Adnan Manzur B Basil T. Darras P Peter B. Kang L Leslie Morrison M Monika Krzesniak-Swinarska J Jean K. Mah T Tiziana E. Mongini F Federica Ricci M Maja von der Hagen R Richard S. Finkel (Center for Experimental Neurotherapeutics, Department of Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, TN) K Kathleen O’Reardon M Matthew Wicklund A Ashutosh Kumar C Craig M. McDonald J Jay J. Han N Nanette Joyce E Erik K. Henricson U Ulrike Schara-Schmidt A Andrea Gangfus E Ekkehard Wilichowski R Richard J. Barohn J Jeffrey M. Statland C Craig Campbell G Giuseppe Vita G Gian Luca Vita J James FHoward I Imelda Hughes H Hugh J. Mcmillan E Elena Pegoraro L Luca Bello W WBryan Burnette M Mathula Thangarajh T Taeun Chang P Paula R. Clemens E Eric P. Hoffman U Utkarsh J. Dang Y Yetrib Hathout

Article Details

Volume / Issue Vol. 15, Issue 1
Published November 14, 2025
ISSN 2045-2322
Publisher Nature Portfolio

Journal Info

Scientific Reports

Nature Portfolio

ISSN: 2045-2322 Open Access Life Sciences

Authors (113)

F

Fatemeh Ahmadiharchegani

R

Rebecca A. Tobin

C

Chiara Degan

A

Ahmed Naveed

M

Michela Guglieri

A

Albert Jiménez-Requena

S

Sharon I. de Vries

C

Cristina Al-Khalili Szigyarto

P

Pietro Spitali

R

Roula Tsonaka

Y

Yuri E. M. van der Burgt

J

Jordi Diaz-Manera

J

Jesse M. Damsker

S

Seth J. Perlman

E

Edward C. Smith

I

Iain Horrocks

N

Nicolas Deconinck

N

Nathalie M. Goemans

J

Jana Haberlova

L

Laurel Mengle-Gaw

B

Benjamin D. Schwartz

A

Amy Harper

L

Liesbeth De Waele

D

Diana Castro

M

Michele L. Yang

M

Monique M. Ryan

E

Erica Goude

M

Mar Tulinius

R

Richard I. Webster

N

Nancy Kuntz

V

Vamshi K. Rao

A

Annie M. Sbrocchi

K

Kathryn A. Selby

M

Migvis Monduy

Y

Yoram Nevo

J

Juan J. Vilchez

A

Andres Nascimento-Osorio

E

Erik H. Niks

I

Imelda JM De Groot

M

Marina Katsalouli

J

John N. Van DenAnker

L

Leanne M. Ward

Children’s Hospital at London Health Sciences Centre, London, ON, Canada

M

Mika Leinonen

T

Tina Duong

C

Carolina Tesi Rocha

M

MD Andrea L. D’Alessandro

L

Lauren P. Morgenroth

K

Kate Bushby

M

Michael P. McDermott

K

Kimberly A. Hart

R

Rabi Tawil

W

William B. Martens

B

Barbara E. Herr

E

Elaine McColl

C

Chris Speed

J

Jennifer Wilkinson

J

Janbernd Kirschner

W

Wendy M. King

M

Michelle Eagle

M

Mary W. Brown

T

Tracey Willis

R

Robert C. Griggs

V

Volker Straub

H

Henriette van Ruiten

A

Anne-Marie Childs

E

Emma Ciafaloni

University of Rochester, Rochester, NY

P

Perry B. Shieh

S

Stefan Spinty

L

Lorenzo Maggi

G

Giovanni Baranello

R

Russell J. Butterfield

I

IA Horrocks

H

Helen Roper

Z

Zoya Alhaswani

K

Kevin M. Flanigan

Nationwide Children’s Hospital, Columbus, OH

N

Nancy L. Kuntz

A

Adnan Manzur

B

Basil T. Darras

P

Peter B. Kang

L

Leslie Morrison

M

Monika Krzesniak-Swinarska

J

Jean K. Mah

T

Tiziana E. Mongini

F

Federica Ricci

M

Maja von der Hagen

R

Richard S. Finkel

Center for Experimental Neurotherapeutics, Department of Pediatric Medicine, St. Jude Children’s Research Hospital, Memphis, TN

K

Kathleen O’Reardon

M

Matthew Wicklund

A

Ashutosh Kumar

C

Craig M. McDonald

J

Jay J. Han

N

Nanette Joyce

E

Erik K. Henricson

U

Ulrike Schara-Schmidt

A

Andrea Gangfus

E

Ekkehard Wilichowski

R

Richard J. Barohn

J

Jeffrey M. Statland

C

Craig Campbell

G

Giuseppe Vita

G

Gian Luca Vita

J

James FHoward

I

Imelda Hughes

H

Hugh J. Mcmillan

E

Elena Pegoraro

L

Luca Bello

W

WBryan Burnette

M

Mathula Thangarajh

T

Taeun Chang

P

Paula R. Clemens

E

Eric P. Hoffman

U

Utkarsh J. Dang

Y

Yetrib Hathout